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NCT02742883

A Phase 2 Study of Atengenal (A-10) and Astugenal (AS2-1) in Diffuse, Intrinsic Pontine Glioma (DIPG)

Suspended Phase 2 Last updated 15 September 2025
What this trial tests

Phase 2 trial testing Antineoplaston therapy (Atengenal + Astugenal) in Diffuse, Intrinsic Pontine Glioma in 1 participant. Suspended.

Timeline
13 April 2016
Primary endpoint
1 March 2028
1 March 2028

Quick facts

Lead sponsorBurzynski Research Institute
PhasePhase 2
StatusSuspended
Study typeINTERVENTIONAL
Allocationna
Designsingle group
Maskingnone
Primary purposetreatment
Enrollment1
Start date13 April 2016
Primary completion1 March 2028
Estimated completion1 March 2028
Sites1 location across United States

Drugs / interventions tested

Conditions studied

Sponsor

Burzynski Research Institute

Who can join

Adults 3 Months to 99, any sex, with Diffuse, Intrinsic Pontine Glioma. Patients with the condition only — healthy volunteers not accepted.

What's being measured

Primary outcomes are the specific endpoints the trial is designed to prove or disprove.

Sponsor's own description

Current therapies for diffuse, intrinsic pontine glioma (DIPG) provide very limited benefit to the patient. The rationale for the use of Antineoplaston therapy in this protocol study derives from experience with subjects from prior Phase 2 studies and Compassionate Exemption patients treated with Antineoplaston therapy at the Burzynski Clinic. This study is designed to analyze the efficacy and safety of Antineoplaston therapy in five separate DIPG patient cohorts, which are defined by age and prior therapy. This is a two stage study with 20 patients in each cohort being enrolled in the first stage and an additional 20 patients being enrolled in the second stage, if pre-determined efficacy endpoints in the first stage are realized.

Publications & conference data

3 peer-reviewed publications reference this trial (live from Europe PMC):

  1. The Integration of Biology Into the Treatment of Diffuse Intrinsic Pontine Glioma: A Review of the North American Clinical Trial Perspective.
    Clymer J, Kieran MW. · · 2018 · cited 15× · PMID 29868485 · DOI 10.3389/fonc.2018.00169
  2. Importance of immune monitoring approaches and the use of immune checkpoints for the treatment of diffuse intrinsic pontine glioma: From bench to clinic and vice versa (Review).
    Scutti JAB. · · 2018 · cited 8× · PMID 29484440 · DOI 10.3892/ijo.2018.4283
  3. Bench-to-bedside investigations of H3 K27-altered diffuse midline glioma: drug targets and potential pharmacotherapies.
    Rechberger JS, Bouchal SM, Power EA, Nonnenbroich LF, et al · · 2023 · cited 3× · PMID 37897190 · DOI 10.1080/14728222.2023.2277232

Verify or expand the search:

Other trials of Antineoplaston therapy (Atengenal + Astugenal)

Trials testing the same drug.

Other Burzynski Research Institute trials

Trials by the same sponsor.

Verify against primary sources

Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT02742883.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing