Last reviewed · How we verify

NCT02742090

Evaluate the Efficacy and Safety of TGR-1202 in Participants With Chronic Lymphocytic Leukemia Who Are Intolerant to Prior Therapy

Terminated Phase 2 Results posted Last updated 3 July 2024
What this trial tests

Phase 2 trial testing Umbralisib in Chronic Lymphocytic Leukemia in 51 participants. Terminated before completion.

Timeline
21 April 2016
Primary endpoint
10 June 2021
10 June 2021

Quick facts

Lead sponsorTG Therapeutics, Inc.
PhasePhase 2
StatusTerminated
Study typeINTERVENTIONAL
Allocationna
Designsingle group
Maskingnone
Primary purposetreatment
Enrollment51
Start date21 April 2016
Primary completion10 June 2021
Estimated completion10 June 2021
Sites15 locations across United States

Drugs / interventions tested

Conditions studied

Sponsor

TG Therapeutics, Inc. — full company profile →

Who can join

18 and older, any sex, with Chronic Lymphocytic Leukemia. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Progression-free Survival Primary · From Day 1 to the earlier of the first documentation of definitive disease progression or death (Up to 61.7 months)

PFS was defined as the interval from Day 1 to the earlier of the first documentation of definitive disease progression (PD) or death from any cause. Participants who had no event (progression or death) were censored at the day of their last adequate disease assessment.

GroupValue95% CI
Umbralisib19.712.9 – 24.8
Overall Response Rate (ORR) Secondary · Up to 61.7 months

ORR=percent of participants who achieve complete response (CR), or partial response (PR).

GroupValue95% CI
Umbralisib34
Time to Treatment Failure (TTF) Secondary · From Day 1 to discontinuation of treatment for any reason, including disease progression, treatment toxicity, and death (up to approximately 61.7 months)

TTF is defined as a composite endpoint measuring time from Day 1 to discontinuation of treatment for any reason, including disease progression, treatment toxicity, and death. Estimates of median TTF was made using Kaplan-Meier methods.

GroupValue95% CI
Umbralisib13.69.4 – 19.0
Duration of Response (DOR) Secondary · From first documentation of CR or PR till disease progression/death (up to approximately 61.7 months)

DOR defined as the interval from the first documentation of CR or PR to the earlier of the first documentation of definitive disease progression or death from any cause. Estimates of median DOR was made using Kaplan-Meier methods.

GroupValue95% CI
Umbralisib19.48.4 – NA
Number of Participants With Treatment-Emergent Adverse Events (TEAE's) as Assessed by Common Terminology Criteria for Adverse Events Version 4.0 (CTCAE v4.0) Secondary · From first dose of study treatment up to end of study (up to 61.7 months)

An adverse event (AE) is any untoward medical occurrence in a participant or clinical investigation participant administered a pharmaceutical product. An AE does not necessarily have to have a causal relationship with this treatment. An AE can therefore be any unfavorable and unintended sign (including an abnormal laboratory finding, for example), symptom, or disease temporarily associated with the use of a medicinal product, whether or not considered related to the medicinal product. TEAE is any AE that occur after first dosing of study medication and through the end of the study or through 3

GroupValue95% CI
Umbralisib51

Adverse events — posted to ClinicalTrials.gov

Time frame: From first dose of study treatment up to end of study (up to approximately 61.7 months). Reporting threshold: 5%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Umbralisib
Serious: 22/51 (43%)
Deaths: 3/51

Serious adverse events (36 terms)

ReactionSystemUmbralisib
PneumoniaInfections and infestations
Febrile neutropeniaBlood and lymphatic system disorders
InfluenzaInfections and infestations
Atrial fibrillationCardiac disorders
ColitisGastrointestinal disorders
DiarrhoeaGastrointestinal disorders
PancreatitisGastrointestinal disorders
Pancreatitis acuteGastrointestinal disorders
AstheniaGeneral disorders
HypersensitivityImmune system disorders
BronchitisInfections and infestations
COVID-19Infections and infestations
CellulitisInfections and infestations
Intervertebral discitisInfections and infestations
SepsisInfections and infestations
Urinary tract infectionInfections and infestations
Urinary tract infection bacterialInfections and infestations
Humerus fractureInjury, poisoning and procedural complications
Influenza A virus test positiveInvestigations
Platelet count decreasedInvestigations
Transaminases increasedInvestigations
HyperglycaemiaMetabolism and nutrition disorders
HypocalcaemiaMetabolism and nutrition disorders
HypokalaemiaMetabolism and nutrition disorders
HypophosphataemiaMetabolism and nutrition disorders
Other adverse events (34 terms — click to expand)

ReactionSystemUmbralisib
DiarrhoeaGastrointestinal disorders
NauseaGastrointestinal disorders
InsomniaPsychiatric disorders
HeadacheNervous system disorders
FatigueGeneral disorders
ContusionInjury, poisoning and procedural complications
Oedema peripheralGeneral disorders
Aspartate aminotransferase increasedInvestigations
Neutrophil count decreasedInvestigations
Decreased appetiteMetabolism and nutrition disorders
ConstipationGastrointestinal disorders
VomitingGastrointestinal disorders
Upper respiratory tract infectionInfections and infestations
Alanine aminotransferase increasedInvestigations
ArthralgiaMusculoskeletal and connective tissue disorders
DizzinessNervous system disorders
CoughRespiratory, thoracic and mediastinal disorders
RashSkin and subcutaneous tissue disorders
AnaemiaBlood and lymphatic system disorders
PyrexiaGeneral disorders
Blood alkaline phosphatase increasedInvestigations
Platelet count decreasedInvestigations
Rash maculo-papularSkin and subcutaneous tissue disorders
LeukocytosisBlood and lymphatic system disorders
HypokalaemiaMetabolism and nutrition disorders
Back painMusculoskeletal and connective tissue disorders
MyalgiaMusculoskeletal and connective tissue disorders
Pain in extremityMusculoskeletal and connective tissue disorders
ParaesthesiaNervous system disorders
TremorNervous system disorders
Dry mouthGastrointestinal disorders
Neck painMusculoskeletal and connective tissue disorders
DyspnoeaRespiratory, thoracic and mediastinal disorders
PruritusSkin and subcutaneous tissue disorders

Most-reported serious reactions: Pneumonia, Febrile neutropenia, Influenza, Atrial fibrillation, Colitis, Diarrhoea, Pancreatitis, Pancreatitis acute.

Data from ClinicalTrials.gov NCT02742090 adverse events section.

Sponsor's own description

The main objective of this study is to determine the progression free survival of umbralisib in participants who were intolerant to prior BTK (Bruton Tyrosine Kinase) inhibitors (ibrutinib, ACP-196, other) or prior PI3K-delta inhibitors (idelalisib, duvelisib, other).

Publications & conference data

8 peer-reviewed publications reference this trial (live from Europe PMC):

  1. Role of PI3K/AKT pathway in cancer: the framework of malignant behavior.
    Jiang N, Dai Q, Su X, Fu J, et al · · 2020 · cited 419× · PMID 32333246 · DOI 10.1007/s11033-020-05435-1
  2. Toxicities and outcomes of 616 ibrutinib-treated patients in the United States: a real-world analysis.
    Mato AR, Nabhan C, Thompson MC, Lamanna N, et al · · 2018 · cited 333× · PMID 29419429 · DOI 10.3324/haematol.2017.182907
  3. PI3K Inhibitors in Cancer: Clinical Implications and Adverse Effects.
    Mishra R, Patel H, Alanazi S, Kilroy MK, et al · · 2021 · cited 207× · PMID 33801659 · DOI 10.3390/ijms22073464
  4. Outcomes of CLL patients treated with sequential kinase inhibitor therapy: a real world experience.
    Mato AR, Nabhan C, Barr PM, Ujjani CS, et al · · 2016 · cited 159× · PMID 27601462 · DOI 10.1182/blood-2016-05-716977
  5. Current and future treatment strategies in chronic lymphocytic leukemia.
    Patel K, Pagel JM. · · 2021 · cited 60× · PMID 33902665 · DOI 10.1186/s13045-021-01054-w
  6. From Biology to Therapy: The CLL Success Story.
    Yosifov DY, Wolf C, Stilgenbauer S, Mertens D. · · 2019 · cited 48× · PMID 31723816 · DOI 10.1097/hs9.0000000000000175
  7. Small-molecule agents for cancer immunotherapy.
    Wang F, Fu K, Wang Y, Pan C, et al · · 2024 · cited 41× · PMID 38486980 · DOI 10.1016/j.apsb.2023.12.010
  8. Phase 2 study of the safety and efficacy of umbralisib in patients with CLL who are intolerant to BTK or PI3Kδ inhibitor therapy.
    Mato AR, Ghosh N, Schuster SJ, Lamanna N, et al · · 2021 · cited 34× · PMID 33259589 · DOI 10.1182/blood.2020007376

Verify or expand the search:

Other trials of Umbralisib

Trials testing the same drug.

Other recruiting trials for Chronic Lymphocytic Leukemia

Currently open trials in the same condition.

Other TG Therapeutics, Inc. trials

Trials by the same sponsor.

Verify against primary sources

Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT02742090.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing