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NCT02694978

A Phase III Safety Study of Ferumoxytol Compared to Ferric Carboxymaltose for the Treatment of Iron Deficiency Anemia (IDA)

Completed Phase 3 Results posted Last updated 25 July 2023
What this trial tests

Phase 3 trial testing Ferumoxytol in Iron Deficiency Anemia in 2,014 participants. Completed in 17 July 2017.

Timeline
29 February 2016
Primary endpoint
16 January 2017
17 July 2017

Quick facts

Lead sponsorAMAG Pharmaceuticals, Inc.
PhasePhase 3
StatusCompleted
Study typeINTERVENTIONAL
Allocationrandomized
Designparallel
Maskingquadruple
Primary purposetreatment
Enrollment2,014
Start date29 February 2016
Primary completion16 January 2017
Estimated completion17 July 2017
Sites127 locations across Hungary, Poland, Canada, Lithuania, Puerto Rico, United States, Latvia

Drugs / interventions tested

Conditions studied

Sponsor

AMAG Pharmaceuticals, Inc. — full company profile →

Who can join

18 and older, any sex, with Iron Deficiency Anemia. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Participants With Treatment-Emergent (TE) Moderate To Severe Hypersensitivity Reactions (Rxns), Including Anaphylaxis, Or Moderate To Severe Hypotension Primary · Day 1 (after first dosing) through Week 5

All IV iron formulations carry some risk of serious hypersensitivity reactions or anaphylaxis. Signs and symptoms potentially representing hypersensitivity were recorded and adjudicated by a blinded Clinical Events Committee (CEC). Hypotension is defined as a \>30% drop in systolic blood pressure from baseline or decrease of \>20 mmHg for systolic blood pressure. Statistical analysis was only performed on composite data. A summary of serious and all other non-serious adverse events regardless of causality is located in the Reported Adverse Events module.

Moderate hypersensitivity reaction
GroupValue95% CI
Ferumoxytol3
Ferric Carboxymaltose (FCM)6
Severe hypersensitivity reaction
GroupValue95% CI
Ferumoxytol1
Ferric Carboxymaltose (FCM)0
Anaphylaxis
GroupValue95% CI
Ferumoxytol0
Ferric Carboxymaltose (FCM)0
Moderate hypotension
GroupValue95% CI
Ferumoxytol2
Ferric Carboxymaltose (FCM)1
Severe hypotension
GroupValue95% CI
Ferumoxytol0
Ferric Carboxymaltose (FCM)0
Any TE moderate to severe hypersensitivity rxn
GroupValue95% CI
Ferumoxytol6
Ferric Carboxymaltose (FCM)7
Participants With Moderate To Severe Hypersensitivity Reactions, Including Anaphylaxis, Serious Cardiovascular Events, And Death Secondary · Day 1 (after first dosing) through Week 5

All IV iron formulations carry some risk of serious hypersensitivity reactions or anaphylaxis. Signs and symptoms potentially representing hypersensitivity were recorded and adjudicated by a blinded Clinical Events Committee (CEC). A summary of serious and all other non-serious adverse events regardless of causality is located in the Reported Adverse Events module.

Moderate hypersensitivity reaction
GroupValue95% CI
Ferumoxytol3
Ferric Carboxymaltose (FCM)6
Severe hypersensitivity reaction
GroupValue95% CI
Ferumoxytol1
Ferric Carboxymaltose (FCM)0
Anaphylaxis
GroupValue95% CI
Ferumoxytol0
Ferric Carboxymaltose (FCM)0
Serious cardiovascular event
GroupValue95% CI
Ferumoxytol6
Ferric Carboxymaltose (FCM)13
Death
GroupValue95% CI
Ferumoxytol4
Ferric Carboxymaltose (FCM)2
Any moderate to severe hypersensitivity rxn
GroupValue95% CI
Ferumoxytol13
Ferric Carboxymaltose (FCM)20
Mean Change In Hemoglobin From Baseline To Week 5 Secondary · Baseline (Day 1), Week 5

Mean change in hemoglobin from Baseline to Week 5 was calculated for each participant as: Hemoglobin Change = Hemoglobin (Week 5) - Hemoglobin (Baseline). Baseline was defined as the Day 1 value (prior to injection of study drug). The screening or most recent value prior to Day 1 was used for any participant with missing Day 1 information.

GroupValue95% CI
Ferumoxytol1.38± 1.351
Ferric Carboxymaltose (FCM)1.63± 1.535
Mean Change In Hemoglobin Per Gram Of Iron Administered From Baseline To Week 5 Secondary · Baseline (Day 1), Week 5

Mean change in hemoglobin per g of iron administered from Baseline (Day 1) to Week 5 was calculated for each participant as: Hemoglobin Change = Hemoglobin (Week 5) - Hemoglobin (Baseline). Baseline was defined as the Day 1 value (prior to injection of study drug). The screening or most recent value prior to Day 1 was used for any participant with missing Day 1 information.

GroupValue95% CI
Ferumoxytol1.35± 1.353
Ferric Carboxymaltose (FCM)1.10± 1.050

Adverse events — posted to ClinicalTrials.gov

Reporting threshold: 1%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Ferumoxytol
Serious: 36/997 (4%)
Deaths:
Ferric Carboxymaltose (FCM)
Serious: 35/1000 (4%)
Deaths:

Serious adverse events (68 terms)

ReactionSystemFerumoxytolFerric Carboxymaltose (FCM)
SyncopeNervous system disorders
GastroenteritisInfections and infestations
Cardiac failure congestiveCardiac disorders
SeizureNervous system disorders
PneumoniaInfections and infestations
Haemorrhagic anaemiaBlood and lymphatic system disorders
Acute kidney injuryRenal and urinary disorders
Angina pectorisCardiac disorders
Atrial fibrillationCardiac disorders
Osteomyelitis chronicInfections and infestations
Gastric ulcer haemorrhageGastrointestinal disorders
Anaemia vitamin B12 deficiencyBlood and lymphatic system disorders
Cardiorespiratory arrestCardiac disorders
Left ventricular failureCardiac disorders
Abdominal painGastrointestinal disorders
AscitesGastrointestinal disorders
Joint abscessInfections and infestations
Pancreatitis acuteGastrointestinal disorders
Anaphylactic reactionImmune system disorders
Anal abscessInfections and infestations
CellulitisInfections and infestations
SepsisInfections and infestations
Sepsis syndromeInfections and infestations
Anastomotic ulcerInjury, poisoning and procedural complications
Intentional overdoseInjury, poisoning and procedural complications
Other adverse events (20 terms — click to expand)

ReactionSystemFerumoxytolFerric Carboxymaltose (FCM)
HeadacheNervous system disorders
NauseaGastrointestinal disorders
DizzinessNervous system disorders
FatigueGeneral disorders
DiarrhoeaGastrointestinal disorders
PyrexiaGeneral disorders
Abdominal painGastrointestinal disorders
Back painMusculoskeletal and connective tissue disorders
HypophosphataemiaMetabolism and nutrition disorders
DyspnoeaRespiratory, thoracic and mediastinal disorders
FlushingVascular disorders
CoughRespiratory, thoracic and mediastinal disorders
HypertensionVascular disorders
ConstipationGastrointestinal disorders
ArthralgiaMusculoskeletal and connective tissue disorders
VomitingGastrointestinal disorders
UrticariaSkin and subcutaneous tissue disorders
PruritusSkin and subcutaneous tissue disorders
Chest discomfortGeneral disorders
Chest painGeneral disorders

Most-reported serious reactions: Syncope, Gastroenteritis, Cardiac failure congestive, Seizure, Pneumonia, Haemorrhagic anaemia, Acute kidney injury, Angina pectoris.

Data from ClinicalTrials.gov NCT02694978 adverse events section.

Sponsor's own description

To evaluate the safety of 1.020 grams (g) of intravenous (IV) ferumoxytol compared to 1.500 g of IV ferric carboxymaltose (FCM).

Publications & conference data

5 peer-reviewed publications reference this trial (live from Europe PMC):

  1. Randomized trial of intravenous iron-induced hypophosphatemia.
    Wolf M, Chertow GM, Macdougall IC, Kaper R, et al · · 2018 · cited 121× · PMID 30518682 · DOI 10.1172/jci.insight.124486
  2. New Opportunities and Old Challenges in the Clinical translation of Nanotheranostics.
    Gawne PJ, Ferreira M, Papaluca M, Grimm J, et al · · 2023 · cited 112× · PMID 39022623 · DOI 10.1038/s41578-023-00581-x
  3. Comparative safety of intravenous ferumoxytol versus ferric carboxymaltose in iron deficiency anemia: A randomized trial.
    Adkinson NF, Strauss WE, Macdougall IC, Bernard KE, et al · · 2018 · cited 106× · PMID 29417614 · DOI 10.1002/ajh.25060
  4. Clinical data for intravenous iron - debunking the hype around hypersensitivity.
    Achebe M, DeLoughery TG. · · 2020 · cited 25× · PMID 32479668 · DOI 10.1111/trf.15837
  5. Comparative safety of intravenous Ferumoxytol versus Ferric Carboxymaltose for the Treatment of Iron Deficiency Anemia: rationale and study design of a randomized double-blind study with a focus on acute hypersensitivity reactions.
    Adkinson NF, Strauss WE, Bernard K, Kaper RF, et al · · 2017 · cited 8× · PMID 29033620 · DOI 10.2147/jbm.s142236

Verify or expand the search:

Other trials of Ferumoxytol

Trials testing the same drug.

Other recruiting trials for Iron Deficiency Anemia

Currently open trials in the same condition.

Other AMAG Pharmaceuticals, Inc. trials

Trials by the same sponsor.

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