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NCT02472886

Safety and Efficacy of Ledipasvir/Sofosbuvir in Adults With Chronic HCV Infection

Completed Phase 3 Results posted Last updated 16 November 2018
What this trial tests

Phase 3 trial testing LDV/SOF in Hepatitis C Virus Infection in 153 participants. Completed in 30 June 2016.

Timeline
17 June 2015
Primary endpoint
30 March 2016
30 June 2016

Quick facts

Lead sponsorGilead Sciences
PhasePhase 3
StatusCompleted
Study typeINTERVENTIONAL
Allocationnon randomized
Designparallel
Maskingnone
Primary purposetreatment
Enrollment153
Start date17 June 2015
Primary completion30 March 2016
Estimated completion30 June 2016
Sites20 locations across Estonia, Russia

Drugs / interventions tested

Conditions studied

Sponsor

Gilead Sciences — full company profile →

Who can join

18 and older, any sex, with Hepatitis C Virus Infection. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Percentage of Participants With Sustained Virologic Response 12 Weeks After Discontinuation of Therapy (SVR12) Primary · Posttreatment Week 12

SVR12 was defined as HCV RNA \< the lower limit of quantitation (LLOQ) 12 weeks following the last dose of study drug.

GroupValue95% CI
LDV/SOF 8 Weeks (TN, HCV-monoinfected)100.094.6 – 100.0
LDV/SOF 8 Weeks (TN, HCV/HIV-coinfected)96.688.3 – 99.6
LDV/SOF + RBV 12 Weeks (TE, SOF-treated, HCV-monoinfected)96.381.0 – 99.9
Percentage of Participants Who Discontinued Study Drug Due to Any Adverse Event (AE) Primary · Up to 12 weeks
GroupValue95% CI
LDV/SOF 8 Weeks (TN, HCV-monoinfected)0
LDV/SOF 8 Weeks (TN, HCV/HIV-coinfected)0
LDV/SOF + RBV 12 Weeks (TE, SOF-treated, HCV-monoinfected)0
Percentage of Participants With Sustained Virologic Response (SVR) at 4 and 24 Weeks After Discontinuation of Therapy (SVR4 and SVR24) Secondary · Posttreatment Weeks 4 and 24

SVR4 and SVR24 were defined as HCV RNA \< LLOQ at 4 and 24 weeks following the last dose of study drug, respectively.

SVR4
GroupValue95% CI
LDV/SOF 8 Weeks (TN, HCV-monoinfected)100.094.6 – 100.0
LDV/SOF 8 Weeks (TN, HCV/HIV-coinfected)96.688.3 – 99.6
LDV/SOF + RBV 12 Weeks (TE, SOF-treated, HCV-monoinfected)96.381.0 – 99.9
SVR24
GroupValue95% CI
LDV/SOF 8 Weeks (TN, HCV-monoinfected)100.094.6 – 100.0
LDV/SOF 8 Weeks (TN, HCV/HIV-coinfected)96.688.3 – 99.6
LDV/SOF + RBV 12 Weeks (TE, SOF-treated, HCV-monoinfected)96.381.0 – 99.9
Percentage of Participants With HCV RNA < LLOQ on Treatment Secondary · Up to 12 weeks
Week 1
GroupValue95% CI
LDV/SOF 8 Weeks (TN, HCV-monoinfected)20.911.9 – 32.6
LDV/SOF 8 Weeks (TN, HCV/HIV-coinfected)39.026.5 – 52.6
LDV/SOF + RBV 12 Weeks (TE, SOF-treated, HCV-monoinfected)3.70.1 – 19.0
Week 2
GroupValue95% CI
LDV/SOF 8 Weeks (TN, HCV-monoinfected)65.753.1 – 76.8
LDV/SOF 8 Weeks (TN, HCV/HIV-coinfected)69.556.1 – 80.8
LDV/SOF + RBV 12 Weeks (TE, SOF-treated, HCV-monoinfected)59.338.8 – 77.6
Week 4
GroupValue95% CI
LDV/SOF 8 Weeks (TN, HCV-monoinfected)100.094.6 – 100.0
LDV/SOF 8 Weeks (TN, HCV/HIV-coinfected)96.688.3 – 99.6
LDV/SOF + RBV 12 Weeks (TE, SOF-treated, HCV-monoinfected)88.970.8 – 97.6
Week 8
GroupValue95% CI
LDV/SOF 8 Weeks (TN, HCV-monoinfected)100.094.6 – 100.0
LDV/SOF 8 Weeks (TN, HCV/HIV-coinfected)98.390.9 – 100.0
LDV/SOF + RBV 12 Weeks (TE, SOF-treated, HCV-monoinfected)100.087.2 – 100.0
Week 12
GroupValue95% CI
LDV/SOF 8 Weeks (TN, HCV-monoinfected)NANA – NA
LDV/SOF 8 Weeks (TN, HCV/HIV-coinfected)NANA – NA
LDV/SOF + RBV 12 Weeks (TE, SOF-treated, HCV-monoinfected)100.087.2 – 100.0
HCV RNA Change From Day 1 Secondary · Up to 12 weeks
Week 1
GroupValue95% CI
LDV/SOF 8 Weeks (TN, HCV-monoinfected)-3.97± 0.675
LDV/SOF 8 Weeks (TN, HCV/HIV-coinfected)-4.34± 0.626
LDV/SOF + RBV 12 Weeks (TE, SOF-treated, HCV-monoinfected)-4.12± 0.582
Week 2
GroupValue95% CI
LDV/SOF 8 Weeks (TN, HCV-monoinfected)-4.50± 0.687
LDV/SOF 8 Weeks (TN, HCV/HIV-coinfected)-4.76± 0.522
LDV/SOF + RBV 12 Weeks (TE, SOF-treated, HCV-monoinfected)-4.83± 0.630
Week 4
GroupValue95% CI
LDV/SOF 8 Weeks (TN, HCV-monoinfected)-4.74± 0.723
LDV/SOF 8 Weeks (TN, HCV/HIV-coinfected)-4.89± 0.534
LDV/SOF + RBV 12 Weeks (TE, SOF-treated, HCV-monoinfected)-5.08± 0.642
Week 8
GroupValue95% CI
LDV/SOF 8 Weeks (TN, HCV-monoinfected)-4.74± 0.723
LDV/SOF 8 Weeks (TN, HCV/HIV-coinfected)-4.91± 0.536
LDV/SOF + RBV 12 Weeks (TE, SOF-treated, HCV-monoinfected)-5.11± 0.671
Week 12
GroupValue95% CI
LDV/SOF 8 Weeks (TN, HCV-monoinfected)NA± NA
LDV/SOF 8 Weeks (TN, HCV/HIV-coinfected)NA± NA
LDV/SOF + RBV 12 Weeks (TE, SOF-treated, HCV-monoinfected)-5.11± 0.671
Percentage of Participants With Virologic Failure Secondary · Up to Posttreatment Week 24

Virologic failure was defined as * On-treatment virologic failure * confirmed HCV RNA ≥ LLOQ after having previously had HCV RNA \< LLOQ, while on treatment (ie, breakthrough), * confirmed \> 1 log10 IU/mL increase in HCV RNA from nadir while on treatment (ie, rebound), HCV RNA persistently ≥ LLOQ through 8 weeks of treatment (ie, nonresponse) * Relapse * HCV RNA ≥ LLOQ during the posttreatment period having achieved HCV RNA \< LLOQ at end of treatment, confirmed with 2 consecutive values or last available posttreatment measurement

GroupValue95% CI
LDV/SOF 8 Weeks (TN, HCV-monoinfected)0
LDV/SOF 8 Weeks (TN, HCV/HIV-coinfected)3.4
LDV/SOF + RBV 12 Weeks (TE, SOF-treated, HCV-monoinfected)3.7
Percentage of HIV/HCV- Coinfected Participants That Maintain HIV-1 RNA < 50 Copies/mL While on HCV Treatment and at Posttreatment Week 4 Secondary · Up to Posttreatment Week 4
Week 4
GroupValue95% CI
LDV/SOF 8 Weeks (TN, HCV/HIV-coinfected)100.0
Week 8
GroupValue95% CI
LDV/SOF 8 Weeks (TN, HCV/HIV-coinfected)100.0
Posttreatment Week 4
GroupValue95% CI
LDV/SOF 8 Weeks (TN, HCV/HIV-coinfected)97.2
For HIV/HCV- Coinfected Participants, Change From Baseline in CD4 T-cell Count at the End of Treatment and Posttreatment Week 4 Secondary · Up to Posttreatment Week 4
Change at Week 4
GroupValue95% CI
LDV/SOF 8 Weeks (TN, HCV/HIV-coinfected, ARV- Naive)47± 120.5
LDV/SOF 8 Weeks (TN, HCV/HIV-coinfected, ARV Experienced)159± 114.9
Change at Week 8
GroupValue95% CI
LDV/SOF 8 Weeks (TN, HCV/HIV-coinfected, ARV- Naive)45± 122.7
LDV/SOF 8 Weeks (TN, HCV/HIV-coinfected, ARV Experienced)202± 178.1
Change at Posttreatment Week 4
GroupValue95% CI
LDV/SOF 8 Weeks (TN, HCV/HIV-coinfected, ARV- Naive)74± 117.8
LDV/SOF 8 Weeks (TN, HCV/HIV-coinfected, ARV Experienced)172± 114.1

Adverse events — posted to ClinicalTrials.gov

Time frame: Up to 12 weeks plus 30 days. Reporting threshold: 5%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

LDV/SOF 8 Weeks (TN, HCV-monoinfected)
Serious: 0/67 (0%)
Deaths: 0/67
LDV/SOF 8 Weeks (TN, HCV/HIV-coinfected)
Serious: 0/59 (0%)
Deaths: 0/59
LDV/SOF + RBV 12 Weeks (TE, SOF-treated, HCV-monoinfected)
Serious: 0/27 (0%)
Deaths: 0/27
Other adverse events (6 terms — click to expand)

ReactionSystemLDV/SOF 8 Weeks (TN, HCV-m…LDV/SOF 8 Weeks (TN, HCV/H…LDV/SOF + RBV 12 Weeks (TE…
HeadacheNervous system disorders
DyspepsiaGastrointestinal disorders
Abdominal pain upperGastrointestinal disorders
AstheniaGeneral disorders
Blood bilirubin increasedInvestigations
IrritabilityPsychiatric disorders

Data from ClinicalTrials.gov NCT02472886 adverse events section.

Sponsor's own description

The primary objectives of this study are to evaluate the antiviral efficacy, safety, and tolerability of ledipasvir/sofosbuvir (LDV/SOF) fixed dose combination (FDC) with or without ribavirin (RBV) in adults with chronic hepatitis C virus (HCV) infection.

Publications & conference data

1 peer-reviewed publication reference this trial (live from Europe PMC):

  1. Ledipasvir-Sofosbuvir for 8 Weeks in Non-Cirrhotic Patients with Previously Untreated Genotype 1 HCV Infection ± HIV-1 Co-Infection.
    Isakov V, Gankina N, Morozov V, Kersey K, et al · · 2018 · cited 9× · PMID 29177645 · DOI 10.1007/s40261-017-0606-0

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Other trials of LDV/SOF

Trials testing the same drug.

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