Last reviewed · How we verify

NCT02323646

Safety and Efficacy of Telapristone Acetate (Proellex®) Administered Vaginally for the Treatment of Uterine Fibroids

Completed Phase 2 Results posted Last updated 25 June 2019
What this trial tests

Phase 2 trial testing Placebo in Uterine Fibroids in 42 participants. Completed in 6 April 2017.

Timeline
12 February 2015
Primary endpoint
6 April 2017
6 April 2017

Quick facts

Lead sponsorRepros Therapeutics Inc.
PhasePhase 2
StatusCompleted
Study typeINTERVENTIONAL
Allocationrandomized
Designparallel
Maskingquadruple
Primary purposetreatment
Enrollment42
Start date12 February 2015
Primary completion6 April 2017
Estimated completion6 April 2017
Sites8 locations across United States

Drugs / interventions tested

Conditions studied

Sponsor

Repros Therapeutics Inc. — full company profile →

Who can join

Adults 18 to 47, female only, with Uterine Fibroids. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Percentage of Participants in Amenorrhea at the End of Treatment Course 1 Primary · At the end of 18-weeks Treatment Course 1

Amenorrhea was defined as any 28-day period during treatment (not including the ODI) without a bleeding intensity score \>1. Participants were provided with a daily diary and Pictorial Blood Loss Assessment Chart (PBAC) to record information about the menstrual blood loss (MBL). Bleeding intensity was graded on a 5-point scale where: 1=spotting to 5=heavy bleeding.

GroupValue95% CI
Placebo0.0
Telapristone Acetate 6 mg53.8
Telapristone Acetate 12 mg46.7
Percentage of Participants in Amenorrhea at the End of Treatment Course 2 Secondary · At the end of 18-weeks Treatment Course 2

Amenorrhea was defined as any 28-day period during treatment (not including the ODI) without a bleeding intensity score \>1 after 2 courses of treatment. Participants were provided with a daily diary and (PBAC) to record information about the MBL. Bleeding intensity was graded on a 5-point scale where: 1=spotting to 5=heavy bleeding.

GroupValue95% CI
Placebo7.1
Telapristone Acetate 6 mg46.2
Telapristone Acetate 12 mg46.7
Percentage Change in PBAC Scores From Baseline to the End of Treatment Courses 1 and 2 Secondary · Baseline (No treatment period) to the end of 18-weeks Treatment Course 1 and the end of 18-weeks Treatment Course 2

Uterine bleeding was assessed with the use of the PBAC, a validated self-reporting method to estimate menstrual blood loss. Participants recorded daily the number of tampons and towels used and the degree to which individual items were soiled with blood (plus small or large clots). Pictorial scores range from score 1 for slightly stained tampon/towel, 5 for a partially stained tampon/towel, 10 for a completely saturated tampon, 20 for a completely saturated towel, and 5 for each episode of flooding and for each blood clot larger than a quarter in size. Total score can range from 0 (no bleeding

Percentage Change from BL: Course 1
GroupValue95% CI
Placebo-1.21± 100.850
Telapristone Acetate 6 mg-55.43± 87.522
Telapristone Acetate 12 mg-43.85± 82.634
Percentage Change from BL: Course 2
GroupValue95% CI
Placebo-43.52± 37.967
Telapristone Acetate 6 mg-91.02± 18.367
Telapristone Acetate 12 mg-77.42± 34.762
Percentage Change in Transformed Total Uterine Fibroid System Quality of Life Survey System Severity (UFS-SSS) Score From Baseline to the End of Treatment Courses 1 and 2 and the Course 2 Week 24 Follow-up Visit Secondary · Baseline (No treatment period) to the end of 18-weeks Treatment Course 1, the end of 18-weeks Treatment Course 2 and the Course 2 Week 24 Follow-up Visit

UFS-SSS is an 8 question assessment tool used to measure symptom severity and has been validated as a three month look back questionnaire. Each question was answered on a 5-point scale where 1=Not at all to 5=A very great deal. The sum of the total scores was transformed to a range of 0=no symptoms (best) to 100=most severe symptoms (worst). A negative percentage change from Baseline indicates improvement.

Percentage Change from BL: Course 1
GroupValue95% CI
Placebo-33.54± 30.981
Telapristone Acetate 6 mg-49.68± 37.927
Telapristone Acetate 12 mg-42.27± 45.842
Percentage Change from BL: Course 2
GroupValue95% CI
Placebo-31.11± 33.577
Telapristone Acetate 6 mg-43.69± 35.919
Telapristone Acetate 12 mg-37.98± 46.287
Percentage Change: Course 2, Week 24 Follow-up
GroupValue95% CI
Placebo-37.38± 30.153
Telapristone Acetate 6 mg-26.90± 26.126
Telapristone Acetate 12 mg-14.66± 41.842
Percentage Change in the Individual UFS-SSS Subscale Score Question 1 From Baseline to the End of Treatment Courses 1 and 2 and the Course 2 Week 24 Follow-up Visit Secondary · Baseline (No treatment period) to the end of 18-weeks Treatment Course 1, the end of 18-weeks Treatment Course 2 and the Course 2 Week 24 Follow-up Visit

UFS-SSS is an 8 question assessment tool used to measure symptom severity and has been validated as a three month look back questionnaire. The participant answered UFS-SSS subscale question 1: During the previous 3 months how distressed were you by "heavy bleeding during your menstrual period"? using a 5-point scale where 1=Not at all to 5=A very great deal. A negative percentage change from Baseline indicates improvement.

Percentage Change from BL: Course 1
GroupValue95% CI
Placebo-19.58± 27.672
Telapristone Acetate 6 mg-52.50± 33.811
Telapristone Acetate 12 mg-53.75± 28.052
Percentage Change from BL: Course 2
GroupValue95% CI
Placebo-21.00± 30.074
Telapristone Acetate 6 mg-55.00± 34.319
Telapristone Acetate 12 mg-60.50± 27.330
Percentage Change: Course 2, Week 24 Follow-up
GroupValue95% CI
Placebo-31.67± 41.003
Telapristone Acetate 6 mg-23.89± 31.798
Telapristone Acetate 12 mg-22.22± 26.471
Percentage Change in the Individual UFS-SSS Subscale Score Question 2 From Baseline to the End of Treatment Courses 1 and 2 and the Course 2 Week 24 Follow-up Visit Secondary · Baseline (No treatment period) to the end of 18-weeks Treatment Course 1, the end of 18-weeks Treatment Course 2 and the Course 2 Week 24 Follow-up Visit

UFS-SSS is an 8 question assessment tool used to measure symptom severity and has been validated as a three month look back questionnaire. The participant answered UFS-SSS subscale question 2: During the previous 3 months how distressed were you by "passing blood clots during your menstrual period"? using a 5-point scale where 1=Not at all to 5=A very great deal. A negative percentage change from Baseline indicates improvement.

Percentage Change from BL: Course 1
GroupValue95% CI
Placebo-34.03± 28.431
Telapristone Acetate 6 mg-49.03± 36.205
Telapristone Acetate 12 mg-21.81± 108.137
Percentage Change from BL: Course 2
GroupValue95% CI
Placebo-30.67± 26.646
Telapristone Acetate 6 mg-43.83± 40.484
Telapristone Acetate 12 mg-45.00± 57.542
Percentage Change: Course 2, Week 24 Follow-up
GroupValue95% CI
Placebo-45.00± 29.686
Telapristone Acetate 6 mg6.85± 47.232
Telapristone Acetate 12 mg2.78± 116.916
Percentage Change in the Individual UFS-SSS Subscale Score Question 3 From Baseline to the End of Treatment Courses 1 and 2 and the Course 2 Week 24 Follow-up Visit Secondary · Baseline (No treatment period) to the end of 18-weeks Treatment Course 1, the end of 18-weeks Treatment Course 2 and the Course 2 Week 24 Follow-up Visit

UFS-SSS is an 8 question assessment tool used to measure symptom severity and has been validated as a three month look back questionnaire. The participant answered UFS-SSS subscale question 3: During the previous 3 months how distressed were you by "fluctuation in the duration of your menstrual period compared to your previous cycle"? using a 5-point scale where 1=Not at all to 5=A very great deal. A negative percentage change from Baseline indicates improvement.

Percentage Change from BL: Course 1
GroupValue95% CI
Placebo-16.39± 26.178
Telapristone Acetate 6 mg-26.81± 37.176
Telapristone Acetate 12 mg21.94± 109.882
Percentage Change from BL: Course 2
GroupValue95% CI
Placebo38.67± 135.664
Telapristone Acetate 6 mg-19.33± 55.729
Telapristone Acetate 12 mg-21.67± 48.305
Percentage Change: Course 2, Week 24 Follow-up
GroupValue95% CI
Placebo3.70± 62.086
Telapristone Acetate 6 mg14.44± 37.118
Telapristone Acetate 12 mg20.00± 45.826
Percentage Change in the Individual UFS-SSS Subscale Score Question 4 From Baseline to the End of Treatment Courses 1 and 2 and the Course 2 Week 24 Follow-up Visit Secondary · Baseline (No treatment period) to the end of 18-weeks Treatment Course 1, the end of 18-weeks Treatment Course 2 and the Course 2 Week 24 Follow-up Visit

UFS-SSS is an 8 question assessment tool used to measure symptom severity and has been validated as a three month look back questionnaire. The participant answered UFS-SSS subscale question 4: During the previous 3 months how distressed were you by "fluctuation in the length of your monthly cycle compared to your previous cycles"? using a 5-point scale where 1=Not at all to 5=A very great deal. A negative percentage change from Baseline indicates improvement.

Percentage Change from BL: Course 1
GroupValue95% CI
Placebo-29.31± 25.785
Telapristone Acetate 6 mg-19.44± 65.452
Telapristone Acetate 12 mg65.28± 136.090
Percentage Change from BL: Course 2
GroupValue95% CI
Placebo10.17± 45.443
Telapristone Acetate 6 mg-40.50± 35.677
Telapristone Acetate 12 mg51.67± 165.216
Percentage Change: Course 2, Week 24 Follow-up
GroupValue95% CI
Placebo12.22± 84.967
Telapristone Acetate 6 mg-17.41± 38.838
Telapristone Acetate 12 mg97.22± 120.185
Percentage Change in the Individual UFS-SSS Subscale Score Question 5 From Baseline to the End of Treatment Courses 1 and 2 and the Course 2 Week 24 Follow-up Visit Secondary · Baseline (No treatment period) to the end of 18-weeks Treatment Course 1, the end of 18-weeks Treatment Course 2 and the Course 2 Week 24 Follow-up Visit

UFS-SSS is an 8 question assessment tool used to measure symptom severity and has been validated as a three month look back questionnaire. The participant answered UFS-SSS subscale question 5: During the previous 3 months how distressed were you by "feeling tightness or pressure in your pelvic area"? using a 5-point scale where 1=Not at all to 5=A very great deal. A negative percentage change from Baseline indicates improvement.

Percentage Change from BL: Course 1
GroupValue95% CI
Placebo-33.61± 36.054
Telapristone Acetate 6 mg-41.11± 30.939
Telapristone Acetate 12 mg-53.33± 27.220
Percentage Change from BL: Course 2
GroupValue95% CI
Placebo-33.83± 29.419
Telapristone Acetate 6 mg-36.83± 36.847
Telapristone Acetate 12 mg-10.67± 57.811
Percentage Change: Course 2, Week 24 Follow-up
GroupValue95% CI
Placebo-27.22± 42.76
Telapristone Acetate 6 mg-7.04± 49.137
Telapristone Acetate 12 mg0.37± 66.378
Percentage Change in the Individual UFS-SSS Subscale Score Question 6 From Baseline to the End of Treatment Courses 1 and 2 and the Course 2 Week 24 Follow-up Visit Secondary · Baseline (No treatment period) to the end of 18-weeks Treatment Course 1, the end of 18-weeks Treatment Course 2 and the Course 2 Week 24 Follow-up Visit

UFS-SSS is an 8 question assessment tool used to measure symptom severity and has been validated as a three month look back questionnaire. The participant answered UFS-SSS subscale question 6: During the previous 3 months how distressed were you by "frequent urination during the daytime hours"? using a 5-point scale where 1=Not at all to 5=A very great deal. A negative percentage change from Baseline indicates improvement.

Percentage Change from BL: Course 1
GroupValue95% CI
Placebo-19.72± 32.943
Telapristone Acetate 6 mg-25.97± 24.365
Telapristone Acetate 12 mg-40.28± 26.235
Percentage Change from BL: Course 2
GroupValue95% CI
Placebo-30.83± 29.400
Telapristone Acetate 6 mg-27.50± 32.272
Telapristone Acetate 12 mg-25.67± 50.511
Percentage Change: Course 2, Week 24 Follow-up
GroupValue95% CI
Placebo-17.59± 35.080
Telapristone Acetate 6 mg-8.15± 35.711
Telapristone Acetate 12 mg-17.41± 35.080
Percentage Change in the Individual UFS-SSS Subscale Score Question 7 From Baseline to the End of Treatment Courses 1 and 2 and the Course 2 Week 24 Follow-up Visit Secondary · Baseline (No treatment period) to the end of 18-weeks Treatment Course 1, the end of 18-weeks Treatment Course 2 and the Course 2 Week 24 Follow-up Visit

UFS-SSS is an 8 question assessment tool used to measure symptom severity and has been validated as a three month look back questionnaire. The participant answered UFS-SSS subscale question 7: During the previous 3 months how distressed were you by "frequent nighttime urination"? using a 5-point scale where 1=Not at all to 5=A very great deal. A negative percentage change from Baseline indicates improvement.

Percentage Change from BL: Course 1
GroupValue95% CI
Placebo-30.83± 26.443
Telapristone Acetate 6 mg-29.03± 32.539
Telapristone Acetate 12 mg-30.69± 41.209
Percentage Change from BL: Course 2
GroupValue95% CI
Placebo-31.83± 29.819
Telapristone Acetate 6 mg-45.17± 24.999
Telapristone Acetate 12 mg-7.67± 59.277
Percentage Change: Course 2, Week 24 Follow-up
GroupValue95% CI
Placebo-36.30± 24.463
Telapristone Acetate 6 mg-33.15± 20.008
Telapristone Acetate 12 mg-27.59± 39.678
Percentage Change in the Individual UFS-SSS Subscale Score Question 8 From Baseline to the End of Treatment Courses 1 and 2 and the Course 2 Week 24 Follow-up Visit Secondary · Baseline (No treatment period) to the end of 18-weeks Treatment Course 1, the end of 18-weeks Treatment Course 2 and the Course 2 Week 24 Follow-up Visit

UFS-SSS is an 8 question assessment tool used to measure symptom severity and has been validated as a three month look back questionnaire. The participant answered UFS-SSS subscale question 8: During the previous 3 months how distressed were you by "feeling fatigued"? using a 5-point scale where 1=Not at all to 5=A very great deal. A negative percentage change from Baseline indicates improvement.

Percentage Change from BL: Course 1
GroupValue95% CI
Placebo-30.42± 27.174
Telapristone Acetate 6 mg-40.69± 29.759
Telapristone Acetate 12 mg-38.33± 65.308
Percentage Change from BL: Course 2
GroupValue95% CI
Placebo-28.33± 25.784
Telapristone Acetate 6 mg-32.33± 28.976
Telapristone Acetate 12 mg-27.50± 37.509
Percentage Change: Course 2, Week 24 Follow-up
GroupValue95% CI
Placebo-27.59± 27.299
Telapristone Acetate 6 mg-22.59± 19.421
Telapristone Acetate 12 mg-12.22± 29.059

Adverse events — posted to ClinicalTrials.gov

Time frame: From first dose of study drug through 30 days after the last dose of study drug (approximately 46 weeks). Reporting threshold: 5%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Placebo
Serious: 2/14 (14%)
Deaths: 0/14
Telapristone Acetate 6 mg
Serious: 2/13 (15%)
Deaths: 0/13
Telapristone Acetate 12 mg
Serious: 2/15 (13%)
Deaths: 0/15

Serious adverse events (6 terms)

ReactionSystemPlaceboTelapristone Acetate 6 mgTelapristone Acetate 12 mg
AnaemiaBlood and lymphatic system disorders
Iron deficiency anaemiaBlood and lymphatic system disorders
Chest injuryInjury, poisoning and procedural complications
Aspartate aminotransferase increasedInvestigations
Uterine leiomyomaNeoplasms benign, malignant and unspecified (incl cysts and polyps)
AlcoholismPsychiatric disorders
Other adverse events (74 terms — click to expand)

ReactionSystemPlaceboTelapristone Acetate 6 mgTelapristone Acetate 12 mg
Endometrial hypertrophyReproductive system and breast disorders
Cervical dysplasiaReproductive system and breast disorders
Abdominal pain lowerGastrointestinal disorders
ConstipationGastrointestinal disorders
NauseaGastrointestinal disorders
FatigueGeneral disorders
Hot flushGeneral disorders
PyrexiaGeneral disorders
Bacterial vaginosisInfections and infestations
Fungal infectionInfections and infestations
SinusitisInfections and infestations
Upper respiratory tract infectionInfections and infestations
Vulvovaginal mycotic infectionInfections and infestations
Back painMusculoskeletal and connective tissue disorders
HeadacheNervous system disorders
DysmenorrhoeaReproductive system and breast disorders
Vaginal dischargeReproductive system and breast disorders
DizzinessVascular disorders
AnaemiaBlood and lymphatic system disorders
Type 2 diabetes mellitusEndocrine disorders
GlaucomaEye disorders
Periorbital oedemaEye disorders
Abdominal distensionGastrointestinal disorders
Abdominal painGastrointestinal disorders
Abdominal pain upperGastrointestinal disorders
DiarrhoeaGastrointestinal disorders
Catheter site inflammationGeneral disorders
Influenza like illnessGeneral disorders
MetaplasiaGeneral disorders
Oedema peripheralGeneral disorders
AsthmaImmune system disorders
HypersensitivityImmune system disorders
Seasonal allergyImmune system disorders
CystitisInfections and infestations
Fungal skin infectionInfections and infestations
Pelvic inflammatory diseaseInfections and infestations
Urinary tract infectionInfections and infestations
Viral upper respiratory tract infectionInfections and infestations
Vulvovaginal candidiasisInfections and infestations
Vulvovaginitis trichomonalInfections and infestations

Most-reported serious reactions: Anaemia, Iron deficiency anaemia, Chest injury, Aspartate aminotransferase increased, Uterine leiomyoma, Alcoholism.

Data from ClinicalTrials.gov NCT02323646 adverse events section.

Sponsor's own description

The primary objective of this study is to determine the safety and efficacy of two vaginal doses of Proellex® administered for up to 2 courses of treatment (18 weeks each), each separated by an Off-Drug Interval (ODI), to premenopausal women with symptomatic uterine fibroids.

Publications & conference data

3 peer-reviewed publications reference this trial (live from Europe PMC):

  1. Selective Progesterone Receptor Modulators-Mechanisms and Therapeutic Utility.
    Islam MS, Afrin S, Jones SI, Segars J. · · 2020 · cited 97× · PMID 32365199 · DOI 10.1210/endrev/bnaa012
  2. Selective progesterone receptor modulators (SPRMs) for uterine fibroids.
    Murji A, Whitaker L, Chow TL, Sobel ML. · · 2017 · cited 42× · PMID 28444736 · DOI 10.1002/14651858.cd010770.pub2
  3. Local Transdermal Delivery of Telapristone Acetate Through Breast Skin, Compared With Oral Treatment: A Randomized Double-Blind, Placebo-Controlled Phase II Trial.
    Lee O, Pilewskie M, Karlan S, Tull MB, et al · · 2021 · cited 14× · PMID 32996592 · DOI 10.1002/cpt.2041

Verify or expand the search:

Other trials of Telapristone Acetate

Trials testing the same drug.

Other recruiting trials for Uterine Fibroids

Currently open trials in the same condition.

Other Repros Therapeutics Inc. trials

Trials by the same sponsor.

Verify against primary sources

Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT02323646.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing