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NCT02009761

Multiple Rising Does Study (Subcutaneous Doses) of BI 655064 in Male and Female Patients With Chronic Primary Immune Thrombocytopenic Purpura (ITP).

Terminated Phase 1 Results posted Last updated 15 March 2024
What this trial tests

Phase 1 trial testing BI 655064 in Purpura, Thrombocytopenic, Idiopathic in 6 participants. Terminated before completion.

Timeline
18 December 2013
Primary endpoint
26 April 2016
26 April 2016

Quick facts

Lead sponsorBoehringer Ingelheim
PhasePhase 1
StatusTerminated
Study typeINTERVENTIONAL
Allocationna
Designsingle group
Maskingnone
Primary purposetreatment
Enrollment6
Start date18 December 2013
Primary completion26 April 2016
Estimated completion26 April 2016
Sites2 locations across United States

Drugs / interventions tested

Conditions studied

Sponsor

Boehringer Ingelheim — full company profile →

Who can join

18 and older, any sex, with Purpura, Thrombocytopenic, Idiopathic. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Number of Patients With Response in Platelet Count Primary · Up to 12 weeks.

This outcome measure presents number of patients with a response in platelet count. Response was defined as: \[A\] An increase in platelet count by greater than 20 x 10\^9/L from baseline at any time-point between Week 1 and Week 12, and \[B\] Platelet count above 50 x 10\^9/L at any time point between Week 1 and Week 12 with no rescue therapy. Baseline was defined as the platelet count at Visit 2 before administration of BI 655064. In case the patient fulfilled only one of the conditions, he/she was considered a non-responder.

No
GroupValue95% CI
BI 655064 120 mg / 180 mg5
Yes
GroupValue95% CI
BI 655064 120 mg / 180 mg1
Number of Subjects With Drug-related Adverse Events Secondary · From first drug administration until end of the Residual Effect Period (REP), up to 6 weeks.

Number of participants with investigator defined drug-related adverse events (AEs) is reported.

GroupValue95% CI
BI 655064 120 mg / 180 mg1
Number of Patients Reaching the Cut-off Point for Immune Thrombocytopenic Purpura [ITP] Secondary · Up to 12 weeks.

This outcome measure presents the number of patients reaching the cut-off point for ITP, which was defined as: \[A\] Platelet count ≥ 100 x 10\^9/L at any time point between Week 1 and Week 12.

No
GroupValue95% CI
BI 655064 120 mg / 180 mg6
Yes
GroupValue95% CI
BI 655064 120 mg / 180 mg0

Adverse events — posted to ClinicalTrials.gov

Time frame: From first drug administration until end of the Residual Effect Period (REP), up to 6 weeks.. Reporting threshold: 5%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

BI 655064 120 mg / 180 mg
Serious: 0/6 (0%)
Deaths: 0/6
Other adverse events (18 terms — click to expand)

ReactionSystemBI 655064 120 mg / 180 mg
Platelet count decreasedInvestigations
Upper respiratory tract infectionInfections and infestations
HeadacheNervous system disorders
PetechiaeSkin and subcutaneous tissue disorders
Conjunctival haemorrhageEye disorders
FlatulenceGastrointestinal disorders
Mouth haemorrhageGastrointestinal disorders
HerniaGeneral disorders
ContusionInjury, poisoning and procedural complications
HypokalaemiaMetabolism and nutrition disorders
HypophosphataemiaMetabolism and nutrition disorders
ArthralgiaMusculoskeletal and connective tissue disorders
Musculoskeletal painMusculoskeletal and connective tissue disorders
EpistaxisRespiratory, thoracic and mediastinal disorders
HaemoptysisRespiratory, thoracic and mediastinal disorders
EcchymosisSkin and subcutaneous tissue disorders
Skin irritationSkin and subcutaneous tissue disorders
HaemorrhageVascular disorders

Data from ClinicalTrials.gov NCT02009761 adverse events section.

Sponsor's own description

BI 655064 will be administered subcutaneously once weekly in patients with immune thrombocytopenic purpura (ITP) for up to 12 weeks.

Publications & conference data

2 peer-reviewed publications reference this trial (live from Europe PMC):

  1. Emerging Therapies in Immune Thrombocytopenia.
    Audia S, Bonnotte B, Bonnotte B. · · 2021 · cited 44× · PMID 33801294 · DOI 10.3390/jcm10051004
  2. Novel Therapies to Address Unmet Needs in ITP.
    Mingot-Castellano ME, Bastida JM, Caballero-Navarro G, Entrena Ureña L, et al · · 2022 · cited 21× · PMID 35890078 · DOI 10.3390/ph15070779

Verify or expand the search:

Other trials of BI 655064

Trials testing the same drug.

Other Boehringer Ingelheim trials

Trials by the same sponsor.

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Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT02009761.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing