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NCT01969435

Study of Melphalan HCl for Injection (Propylene Glycol-free), Carmustine, Etoposide, Cytarabine (BEAM Regimen) and Autologous Stem Cell Transplantation for Lymphoma

Completed Phase 2 Results posted Last updated 13 February 2018
What this trial tests

Phase 2 trial testing Carmustine in Hodgkin Disease in 50 participants. Completed in 31 May 2017.

Timeline
19 March 2014
Primary endpoint
30 September 2015
31 May 2017

Quick facts

Lead sponsorWashington University School of Medicine
PhasePhase 2
StatusCompleted
Study typeINTERVENTIONAL
Allocationna
Designsingle group
Maskingnone
Primary purposetreatment
Enrollment50
Start date19 March 2014
Primary completion30 September 2015
Estimated completion31 May 2017
Sites1 location across United States

Drugs / interventions tested

Conditions studied

Sponsor

Washington University School of Medicine

Who can join

Adults 18 to 75, any sex, with Hodgkin Disease or Lymphoma, Non-Hodgkin. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Safety and Toxicity as Measured by Treatment Related Non-hematologic Adverse Events Primary · Day -7 through Day 30

Adverse events will be assessed using the National Cancer Institute (NCI)-CTCAE version 4.0. Number of events, grade 2 or higher, occurring in 10% or greater of participants. Grade 2 diarrhea and Grade 2 nausea/vomiting were not recorded.

Fever neutropenia
GroupValue95% CI
Melphalan, Carmustine, Etoposide, Cytarabine (BEAM)34
Fever
GroupValue95% CI
Melphalan, Carmustine, Etoposide, Cytarabine (BEAM)6
Bacteremia
GroupValue95% CI
Melphalan, Carmustine, Etoposide, Cytarabine (BEAM)7
Clostridium difficile
GroupValue95% CI
Melphalan, Carmustine, Etoposide, Cytarabine (BEAM)3
Respiratory infection
GroupValue95% CI
Melphalan, Carmustine, Etoposide, Cytarabine (BEAM)5
Mucosal infection
GroupValue95% CI
Melphalan, Carmustine, Etoposide, Cytarabine (BEAM)7
Skin infection
GroupValue95% CI
Melphalan, Carmustine, Etoposide, Cytarabine (BEAM)3
Genito-urinary tract infection
GroupValue95% CI
Melphalan, Carmustine, Etoposide, Cytarabine (BEAM)3
Treatment-related Mortality (TRM) Primary · 100 days

TRM is defined as death not due to progressive lymphoma prior to Day 100 after transplant

GroupValue95% CI
Melphalan, Carmustine, Etoposide, Cytarabine (BEAM)0
Efficacy as Measured by Response Rates Secondary · Up to Day 100

* The response rates according to each category of response Complete Response (CR), Partial Response (PR), Stable Disease (SD), and Progressive Disease (PD) will be summarized by the proportion of patients meeting each criterion. * Evaluated using PET or CT scan and Revised Response Criteria for Malignant Lymphoma

Complete response
GroupValue95% CI
Melphalan, Carmustine, Etoposide, Cytarabine (BEAM)84
Partial response
GroupValue95% CI
Melphalan, Carmustine, Etoposide, Cytarabine (BEAM)4
Stable disease
GroupValue95% CI
Melphalan, Carmustine, Etoposide, Cytarabine (BEAM)0
Progressive disease
GroupValue95% CI
Melphalan, Carmustine, Etoposide, Cytarabine (BEAM)12
Disease-free Survival Secondary · 1 year

Percentage of patients who survive without any signs or symptoms of cancer at 1 year.

GroupValue95% CI
Melphalan, Carmustine, Etoposide, Cytarabine (BEAM)7058 – 85
Disease-free Survival Secondary · 2 years

Percentage of patients who survive without any signs or symptoms of cancer at 2 years.

GroupValue95% CI
Melphalan, Carmustine, Etoposide, Cytarabine (BEAM)64
Time to Engraftment (Neutrophil) Secondary · Assessed up to day 30

Time from the date of the transplant to the date of neutrophil engraftment.

GroupValue95% CI
Melphalan, Carmustine, Etoposide, Cytarabine (BEAM)109 – 13
Time to Engraftment (Platelet) Secondary · Assessed up to day 100

Time from the date of transplant to the date of platelet engraftment.

GroupValue95% CI
Melphalan, Carmustine, Etoposide, Cytarabine (BEAM)1912 – 90
Progression-free Survival (PFS) Rate Secondary · 6 months

PFS - Time from start of treatment to the time of progression or death, whichever occurs first.

GroupValue95% CI
Melphalan, Carmustine, Etoposide, Cytarabine (BEAM)8474 – 95
Progression-free Survival Rate (PFS) Secondary · 1 year
GroupValue95% CI
Melphalan, Carmustine, Etoposide, Cytarabine (BEAM)7058 – 85
Relapse Free Survival Secondary · 1 year
GroupValue95% CI
Melphalan, Carmustine, Etoposide, Cytarabine (BEAM)0
Overall Survival (OS) Rate Secondary · Median follow-up 15.4 months (range 4.7-24.6)
GroupValue95% CI
Melphalan, Carmustine, Etoposide, Cytarabine (BEAM)10

Adverse events — posted to ClinicalTrials.gov

Time frame: Reportable adverse events were collected from the first dose of study treatment (Day -7) through the Day +30 visit.. Reporting threshold: 0%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Melphalan, Carmustine, Etoposide, Cytarabine (BEAM)
Serious: 1/50 (2%)
Deaths:

Serious adverse events (1 terms)

ReactionSystemMelphalan, Carmustine, Eto…
Multi-organ failure due to sepsisGeneral disorders
Other adverse events (88 terms — click to expand)

ReactionSystemMelphalan, Carmustine, Eto…
HypophosphatemiaMetabolism and nutrition disorders
Febrile neutropeniaInfections and infestations
Mucositis oralGastrointestinal disorders
HypotensionVascular disorders
HypokalemiaMetabolism and nutrition disorders
HypocalcemiaMetabolism and nutrition disorders
HypoalbuminemiaMetabolism and nutrition disorders
HypoxiaRespiratory, thoracic and mediastinal disorders
DiarrheaGastrointestinal disorders
Rash maculo-papularSkin and subcutaneous tissue disorders
HeadacheNervous system disorders
FeverGeneral disorders
HyperglycemiaMetabolism and nutrition disorders
Abdominal painGastrointestinal disorders
Blood bilirubin increasedInvestigations
DehydrationMetabolism and nutrition disorders
Mucosal infection (oral candidiasis)Infections and infestations
Generalized muscle weaknessMusculoskeletal and connective tissue disorders
HemorrhoidsGastrointestinal disorders
Non-cardiac chest painGeneral disorders
Pain in extremityMusculoskeletal and connective tissue disorders
Weight lossInvestigations
Alanine aminotransferase increasedInvestigations
AnorexiaMetabolism and nutrition disorders
Atrial fibrillationCardiac disorders
Blood-Coagulase-negative staphylococcusInfections and infestations
Bone painMusculoskeletal and connective tissue disorders
Clostridium difficileInfections and infestations
Electrocardiogram QT corrected interval prolongedInvestigations
Gastroesophageal reflux diseaseGastrointestinal disorders
Skin infectionInfections and infestations
Allergic reactionImmune system disorders
Back painMusculoskeletal and connective tissue disorders
Blood-Klebsiella pneumoniaeInfections and infestations
ChillsGeneral disorders
ColitisGastrointestinal disorders
Edema limbsGeneral disorders
FlushingVascular disorders
HSV (oral)Infections and infestations
NauseaGastrointestinal disorders

Most-reported serious reactions: Multi-organ failure due to sepsis.

Data from ClinicalTrials.gov NCT01969435 adverse events section.

Sponsor's own description

Phase II study is being conducted to confirm the safety and efficacy of high-dose Melphalan HCl for Injection (Propylene Glycol-Free) when included in the BEAM regimen for myeloablative conditioning in lymphoma patients undergoing ASCT

Publications & conference data

No peer-reviewed publications indexed yet for this trial. Completed trials usually publish results within 12-18 months.

Verify or expand the search:

Other trials of Carmustine

Trials testing the same drug.

Other recruiting trials for Hodgkin Disease

Currently open trials in the same condition.

Other Washington University School of Medicine trials

Trials by the same sponsor.

Verify against primary sources

Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT01969435.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing