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NCT01732926: Bridalveil

Efficacy and Safety of Idelalisib (GS-1101) in Combination With Bendamustine and Rituximab for Previously Treated Indolent Non-Hodgkin Lymphomas

Terminated Phase 3 Results posted Last updated 16 November 2018
What this trial tests

Phase 3 trial testing Idelalisib in Indolent Non-Hodgkin's Lymphomas in 475 participants. Terminated before completion.

Timeline
2 January 2013
Primary endpoint
17 May 2016
17 May 2016

Quick facts

Lead sponsorGilead Sciences
PhasePhase 3
StatusTerminated
Study typeINTERVENTIONAL
Allocationrandomized
Designparallel
Maskingtriple
Primary purposetreatment
Enrollment475
Start date2 January 2013
Primary completion17 May 2016
Estimated completion17 May 2016
Sites144 locations across France, Italy, Russia, Sweden, Taiwan, United Kingdom, Germany, Israel

Drugs / interventions tested

Conditions studied

Sponsor

Gilead Sciences — full company profile →

Who can join

18 and older, any sex, with Indolent Non-Hodgkin's Lymphomas. Patients with the condition only — healthy volunteers not accepted.

Adverse events — posted to ClinicalTrials.gov

Time frame: Up to 34 months plus 30 days. Reporting threshold: 5%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Idelalisib + Bendamustine + Rituximab
Serious: 229/317 (72%)
Deaths:
Placebo + Bendamustine + Rituximab
Serious: 58/155 (37%)
Deaths:

Serious adverse events (246 terms)

ReactionSystemIdelalisib + Bendamustine …Placebo + Bendamustine + R…
PyrexiaGeneral disorders
Febrile neutropeniaBlood and lymphatic system disorders
PneumoniaInfections and infestations
RashSkin and subcutaneous tissue disorders
PneumonitisRespiratory, thoracic and mediastinal disorders
DiarrhoeaGastrointestinal disorders
Alanine aminotransferase increasedInvestigations
Aspartate aminotransferase increasedInvestigations
ColitisGastrointestinal disorders
Pneumocystis jirovecii pneumoniaInfections and infestations
SepsisInfections and infestations
AnaemiaBlood and lymphatic system disorders
NeutropeniaBlood and lymphatic system disorders
VomitingGastrointestinal disorders
NauseaGastrointestinal disorders
Cytomegalovirus infectionInfections and infestations
Urinary tract infectionInfections and infestations
DehydrationMetabolism and nutrition disorders
Acute kidney injuryRenal and urinary disorders
Respiratory failureRespiratory, thoracic and mediastinal disorders
CellulitisInfections and infestations
Lower respiratory tract infectionInfections and infestations
Infusion related reactionInjury, poisoning and procedural complications
Pleural effusionRespiratory, thoracic and mediastinal disorders
Rash maculo-papularSkin and subcutaneous tissue disorders
Other adverse events (60 terms — click to expand)

ReactionSystemIdelalisib + Bendamustine …Placebo + Bendamustine + R…
NauseaGastrointestinal disorders
DiarrhoeaGastrointestinal disorders
PyrexiaGeneral disorders
NeutropeniaBlood and lymphatic system disorders
RashSkin and subcutaneous tissue disorders
FatigueGeneral disorders
VomitingGastrointestinal disorders
ConstipationGastrointestinal disorders
CoughRespiratory, thoracic and mediastinal disorders
Alanine aminotransferase increasedInvestigations
Decreased appetiteMetabolism and nutrition disorders
Upper respiratory tract infectionInfections and infestations
PruritusSkin and subcutaneous tissue disorders
HypokalaemiaMetabolism and nutrition disorders
AnaemiaBlood and lymphatic system disorders
Aspartate aminotransferase increasedInvestigations
HeadacheNervous system disorders
AstheniaGeneral disorders
Weight decreasedInvestigations
InsomniaPsychiatric disorders
DyspnoeaRespiratory, thoracic and mediastinal disorders
Abdominal painGastrointestinal disorders
ChillsGeneral disorders
Oedema peripheralGeneral disorders
Infusion related reactionInjury, poisoning and procedural complications
ThrombocytopeniaBlood and lymphatic system disorders
Mucosal inflammationGeneral disorders
Rash maculo-papularSkin and subcutaneous tissue disorders
DyspepsiaGastrointestinal disorders
StomatitisGastrointestinal disorders
Urinary tract infectionInfections and infestations
Oropharyngeal painRespiratory, thoracic and mediastinal disorders
Back painMusculoskeletal and connective tissue disorders
DizzinessNervous system disorders
BronchitisInfections and infestations
ArthralgiaMusculoskeletal and connective tissue disorders
Abdominal pain upperGastrointestinal disorders
MyalgiaMusculoskeletal and connective tissue disorders
Dry mouthGastrointestinal disorders
Mouth ulcerationGastrointestinal disorders

Most-reported serious reactions: Pyrexia, Febrile neutropenia, Pneumonia, Rash, Pneumonitis, Diarrhoea, Alanine aminotransferase increased, Aspartate aminotransferase increased.

Data from ClinicalTrials.gov NCT01732926 adverse events section.

Sponsor's own description

The primary objective of this study is to evaluate the addition of idelalisib to bendamustine/rituximab on progression-free survival (PFS) in adults with previously treated indolent non-Hodgkin lymphoma (iNHL). An increased rate of deaths and serious adverse events (SAEs) among participants with front-line chronic lymphocytic leukemia (CLL) and early-line iNHL treated with idelalisib in combination with standard therapies was observed by the independent data monitoring committee (DMC) during regular review of 3 Gilead Phase 3 studies. Gilead reviewed the unblinded data and terminated this study in agreement with the DMC recommendation and in consultation with the US Food and Drug Administration (FDA).

Publications & conference data

8 peer-reviewed publications reference this trial (live from Europe PMC):

  1. Role of PI3K/AKT pathway in cancer: the framework of malignant behavior.
    Jiang N, Dai Q, Su X, Fu J, et al · · 2020 · cited 419× · PMID 32333246 · DOI 10.1007/s11033-020-05435-1
  2. Therapeutic Modulation of Autophagy in Leukaemia and Lymphoma.
    Djavaheri-Mergny M, Giuriato S, Tschan MP, Humbert M. · · 2019 · cited 34× · PMID 30704144 · DOI 10.3390/cells8020103
  3. Phosphoinositide 3-kinase inhibitors in lymphoma.
    Curran E, Smith SM. · · 2014 · cited 32× · PMID 25024054 · DOI 10.1097/cco.0000000000000113
  4. Splenic marginal zone lymphoma: a literature review of diagnostic and therapeutic challenges.
    Santos TSD, Tavares RS, Farias DLC. · · 2017 · cited 30× · PMID 28577652 · DOI 10.1016/j.bjhh.2016.09.014
  5. Idelalisib for the treatment of non-Hodgkin lymphoma.
    Graf SA, Gopal AK. · · 2016 · cited 24× · PMID 26818003 · DOI 10.1517/14656566.2016.1135130
  6. Idelalisib for the treatment of indolent non-Hodgkin lymphoma: a review of its clinical potential.
    Barrientos JC. · · 2016 · cited 19× · PMID 27274288 · DOI 10.2147/ott.s102573
  7. Combinations of idelalisib with rituximab and/or bendamustine in patients with recurrent indolent non-Hodgkin lymphoma.
    de Vos S, Wagner-Johnston ND, Coutre SE, Flinn IW, et al · · 2016 · cited 18× · PMID 29296805 · DOI 10.1182/bloodadvances.2016000976
  8. Novel Targeted Agents in Hodgkin and Non-Hodgkin Lymphoma Therapy.
    Grover NS, Park SI. · · 2015 · cited 15× · PMID 26393619 · DOI 10.3390/ph8030607

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