Long-Term Follow-Up Safety and Preliminary Efficacy Study of Human Central Nervous System Stem Cell (HuCNS-SC®) Transplantation in Subjects With Connatal Pelizaeus-Merzbacher Disease (PMD)

NCT01391637 COMPLETED

The purpose of this study is to determine the long term safety and preliminary effect of HuCNS-SC cells transplanted in subjects with Connatal Pelizaeus-Merzbacher Disease (PMD).

Details

Lead sponsor	StemCells, Inc.
Status	COMPLETED
Enrolment	4
Start date	2011-06
Completion	2016-03

Conditions

• Pelizaeus-Merzbacher Disease
• PMD

Interventions

• HuCNS-SC transplant in the lead-in phase

Primary outcomes

• Incidence of serious adverse events (SAEs), results of physical and neurological examination, laboratory tests and vital signs. — 4 years

Countries

United States