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NCT01349101

A Research Study of Bone Marrow Transplantation From Unrelated or Partially Matched Related Donors

Completed Phase 2 Results posted Last updated 15 December 2025
What this trial tests

Phase 2 trial testing Total Body Irradiation in Hematological Malignancies in 78 participants. Completed in 7 December 2022.

Timeline
10 February 2011
Primary endpoint
31 October 2022
7 December 2022

Quick facts

Lead sponsorSidney Kimmel Comprehensive Cancer Center at Thomas Jefferson University
PhasePhase 2
StatusCompleted
Study typeINTERVENTIONAL
Allocationnon randomized
Designparallel
Maskingnone
Primary purposetreatment
Enrollment78
Start date10 February 2011
Primary completion31 October 2022
Estimated completion7 December 2022
Sites1 location across United States

Drugs / interventions tested

Conditions studied

Sponsor

Sidney Kimmel Comprehensive Cancer Center at Thomas Jefferson University

Who can join

18 and older, any sex, with Hematological Malignancies. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Successful Engraftment Using Cyclophosphamide Post-Transplant Primary · Through 100 days post-transplant

Successful Hematopoietic engraftment will be assessed by determining the incidence of participants who achieve both of the following criteria within the 100 days post-transplant: ANC \>/= 0.5x10e9/L for at least 3 days. Platelet engraftment \>20,000 with no transfusions X 7 days. The incidence will be calculated as the number of participants who meet both engraftment criteria. Results will be presented as a proportion/percentage/probability not as an incidence rate.

GroupValue95% CI
Myeloablative HSCT1.001.00 – 1.00
Reduced Intensity HSCT0.930.86 – 1.00
Cumulative Incidence of Grade III-IV GVHD Secondary · Through 100 days post-transplant

The cumulative incidence of Grade III-IV graft-versus-host disease (GVHD) within 100 days post-transplant will be estimated; goal is less than 10%. The cumulative incidence represents the probability that a participant experiences Grade III-IV GVHD by day 100. Results will be reported as proportion/percentage/probability.

GroupValue95% CI
Myeloablative HSCT0.51520.3312 – 0.6716
Reduced Intensity HSCT0.31110.1820 – 0.4493
Incidence of GVHD Unresponsive to Corticosteroids and Photopheresis Secondary · Through 100 days post-treatment

This outcome will estimate the cumulative incidence (probability) of graft-versus-host disease (GVHD) that is considered unresponsive to corticosteroids and photopheresis within 100 days after treatment; goal is less than 15%. The cumulative incidence will be calculated as the number of participants meeting these criteria. Results will be reported as a proportion/percentage.

GroupValue95% CI
Myeloablative HSCT0.06250.0107 – 0.1838
Reduced Intensity HSCT0.02330.00177 – 0.1072
Transplant-Related Mortality Secondary · 100 days post-transplant

The cumulative incidence of transplant related mortality (TRM) by day 100 post-transplant will be estimated. Assess day 100 transplant-related mortality; goal is less than 15%. TRM is defined as death that results from medical treatment rather than from the underlying disease itself. The cumulative incidence reflects the probability of TRM by day 100. The result will be reported as a proportion/percentage/probability, not an incidence rate.

GroupValue95% CI
Myeloablative HSCT0.09090.0226 – 0.2192
Reduced Intensity HSCT0.19510.0904 – 0.3292

Adverse events — posted to ClinicalTrials.gov

Time frame: Adverse events were recorded for 100 days following transplant.. Reporting threshold: 0%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Myeloablative HSCT
Serious: 5/33 (15%)
Deaths: 3/33
Reduced Intensity HSCT
Serious: 5/45 (11%)
Deaths: 8/45

Serious adverse events (98 terms)

ReactionSystemMyeloablative HSCTReduced Intensity HSCT
Acute Kidney Injury - Grade 4Renal and urinary disorders
Hypoxia - Grade 3Respiratory, thoracic and mediastinal disorders
Hypotension - Grade 4Cardiac disorders
Pneumonitis - Grade 3Infections and infestations
Syncope - Grade 3Nervous system disorders
Hyperbilirubinemia - Grade 4Hepatobiliary disorders
Hypoxia - Grade 4Respiratory, thoracic and mediastinal disorders
increased creatinine - Grade 4Renal and urinary disorders
Respiratory Failure - Grade 4Respiratory, thoracic and mediastinal disorders
Diarrhea - Grade 3Gastrointestinal disorders
Pulmonary Infiltrates - Grade 4Respiratory, thoracic and mediastinal disorders
Respiratory Failure - Grade 5Respiratory, thoracic and mediastinal disorders
Sepsis - Grade 4Infections and infestations
Acute Kidney Injury - Grade 3Renal and urinary disorders
Adenovirus - Grade 3Infections and infestations
altered mental status - grade 4Psychiatric disorders
Angioedema - Grade 4Skin and subcutaneous tissue disorders
Arterial Thrombosis - Grade 3Vascular disorders
Atrial Fibrillation - Grade 2Cardiac disorders
Atrial Fibrillation - Grade 3Cardiac disorders
Atrioventricular block complete - grade 4Cardiac disorders
BK Viremia - Grade 3Infections and infestations
Blood bilirubin increased - Grade 3Hepatobiliary disorders
Candidemia - Grade 3Infections and infestations
Cardiomyopathy - Grade 3Cardiac disorders
Other adverse events (661 terms — click to expand)

ReactionSystemMyeloablative HSCTReduced Intensity HSCT
Fever - Grade 1Immune system disorders
Rash - Grade 1Skin and subcutaneous tissue disorders
Fatigue - Grade 2General disorders
Constipation - Grade 1Gastrointestinal disorders
Edema - Extremities - Grade 1Vascular disorders
Mucositis - Grade 3Gastrointestinal disorders
Hypertension - Grade 2Vascular disorders
Hypotension - Grade 2Cardiac disorders
Insomnia - Grade 1Psychiatric disorders
Diarrhea - Grade 2General disorders
Anxiety - Grade 2Psychiatric disorders
Fever - Grade 2Immune system disorders
Rash - Grade 2Skin and subcutaneous tissue disorders
Diarrhea - Grade 1Gastrointestinal disorders
Anxiety - Grade 1Psychiatric disorders
Pain - Abdominal - Grade 2General disorders
Tachycardia - Grade 1Cardiac disorders
Emesis - Grade 1Gastrointestinal disorders
Rigors - Grade 1Nervous system disorders
Dyspnea - Grade 1Respiratory, thoracic and mediastinal disorders
Fatigue - Grade 3General disorders
Oliguria - Grade 2Renal and urinary disorders
Dizziness - Grade 1Ear and labyrinth disorders
Hyperbilirubinemia - Grade 1Hepatobiliary disorders
Hypertension - Grade 1Vascular disorders
Nausea - Grade 2Gastrointestinal disorders
Pain - Abdominal - Grade 1General disorders
gastroesophageal reflux disease - Grade 2Gastrointestinal disorders
Headache - Grade 2General disorders
Tussis - Grade 1Respiratory, thoracic and mediastinal disorders
Arthraglia - Grade 1Musculoskeletal and connective tissue disorders
Depression - Grade 2Psychiatric disorders
Hypotension - Grade 1Cardiac disorders
Insomnia - Grade 2Psychiatric disorders
Mucositis - Grade 2Gastrointestinal disorders
Pruritus - Grade 1Skin and subcutaneous tissue disorders
Tremor - Grade 1Nervous system disorders
Acute Kidney Injury - Grade 1Renal and urinary disorders
Arthraglia - Grade 2Musculoskeletal and connective tissue disorders
Awakening to Urinate - Grade 1Renal and urinary disorders

Most-reported serious reactions: Acute Kidney Injury - Grade 4, Hypoxia - Grade 3, Hypotension - Grade 4, Pneumonitis - Grade 3, Syncope - Grade 3, Hyperbilirubinemia - Grade 4, Hypoxia - Grade 4, increased creatinine - Grade 4.

Data from ClinicalTrials.gov NCT01349101 adverse events section.

Sponsor's own description

It is hypothesized that engraftment when administering cyclophosphamide post the stem cell infusion will increase, the incidence of graft versus host disease (GVHD) and day 100 mortality will decrease, and the use of cyclophosphamide post stem cell infusion with alternative donors will be as safe and as effective as traditional matched transplants.

Publications & conference data

1 peer-reviewed publication reference this trial (live from Europe PMC):

  1. Achievement of Tolerance Induction to Prevent Acute Graft-vs.-Host Disease.
    Thangavelu G, Blazar BR. · · 2019 · cited 23× · PMID 30906290 · DOI 10.3389/fimmu.2019.00309

Verify or expand the search:

Other trials of Total Body Irradiation

Trials testing the same drug.

Other recruiting trials for Hematological Malignancies

Currently open trials in the same condition.

Other Sidney Kimmel Comprehensive Cancer Center at Thomas Jefferson University trials

Trials by the same sponsor.

Verify against primary sources

Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT01349101.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing