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NCT01027949: FREEDOM-EXT

An Open-Label Extension Trial of UT-15C Sustained-release (SR) in Subjects With Pulmonary Arterial Hypertension

Completed Phase 3 Results posted Last updated 10 May 2021
What this trial tests

Phase 3 trial testing Oral Treprostinil in Pulmonary Arterial Hypertension in 894 participants. Completed in 12 February 2020.

Timeline
16 January 2007
Primary endpoint
12 February 2020
12 February 2020

Quick facts

Lead sponsorUnited Therapeutics
PhasePhase 3
StatusCompleted
Study typeINTERVENTIONAL
Allocationna
Designsingle group
Maskingnone
Primary purposetreatment
Enrollment894
Start date16 January 2007
Primary completion12 February 2020
Estimated completion12 February 2020
Sites134 locations across Italy, Ireland, Poland, Netherlands, Belgium, Sweden, Mexico, Portugal

Drugs / interventions tested

Conditions studied

Sponsor

United Therapeutics — full company profile →

Who can join

12 and older, any sex, with Pulmonary Arterial Hypertension. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Change in Exercise Capacity at Month 12 Primary · From First Visit (Visit 1) to Month 12

Assess the effect of continued therapy with oral treprostinil on exercise capacity as assessed by the change from Baseline in 6-Minute Walk Test (6MWT) after 1 year of treatment. The 6MWT is the clinical standard for assessing subject functional status in the treatment of PAH and has been considered an objective measure of subject functional status by the American Thoracic Society. The distance a subject can walk in 6 minutes is recorded in meters.

GroupValue95% CI
Oral Treprostinil22.0-345.0 – 282.0

Adverse events — posted to ClinicalTrials.gov

Time frame: From the time of subject enrollment until exit from the study (up to 13 years).. Reporting threshold: 5%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Oral Treprostinil
Serious: 547/894 (61%)
Deaths: 174/894

Serious adverse events (401 terms)

ReactionSystemOral Treprostinil
Pulmonary HypertensionRespiratory, thoracic and mediastinal disorders
Right ventricular failureCardiac disorders
PneumoniaInfections and infestations
DyspnoeaRespiratory, thoracic and mediastinal disorders
Acute kidney injuryRenal and urinary disorders
Cardiac failureCardiac disorders
SyncopeNervous system disorders
AnaemiaBlood and lymphatic system disorders
Chest painGeneral disorders
HypotensionVascular disorders
Fluid overloadMetabolism and nutrition disorders
Cardiac failure congestiveCardiac disorders
Atrial fibrillationCardiac disorders
Respiratory failureRespiratory, thoracic and mediastinal disorders
Sudden deathGeneral disorders
Atrial flutterCardiac disorders
DiarrhoeaGastrointestinal disorders
HypoxiaRespiratory, thoracic and mediastinal disorders
Gastrointestinal haemorrhageGastrointestinal disorders
HypokalaemiaMetabolism and nutrition disorders
BronchitisInfections and infestations
Chronic obstructive pulmonary diseaseRespiratory, thoracic and mediastinal disorders
Lower respiratory tract infectionInfections and infestations
NauseaGastrointestinal disorders
GastritisGastrointestinal disorders
Other adverse events (59 terms — click to expand)

ReactionSystemOral Treprostinil
HeadacheNervous system disorders
DiarrhoeaGastrointestinal disorders
NauseaGastrointestinal disorders
FlushingVascular disorders
VomitingGastrointestinal disorders
Pain in jawMusculoskeletal and connective tissue disorders
Pain in extremityMusculoskeletal and connective tissue disorders
DizzinessCardiac disorders
Upper respiratory tract infectionInfections and infestations
DyspnoeaRespiratory, thoracic and mediastinal disorders
FatigueGeneral disorders
Oedema peripheralGeneral disorders
Pulmonary hypertensionRespiratory, thoracic and mediastinal disorders
NasopharyngitisInfections and infestations
CoughRespiratory, thoracic and mediastinal disorders
PalpitationsCardiac disorders
ArthralgiaMusculoskeletal and connective tissue disorders
Right ventricular failureCardiac disorders
Chest painGeneral disorders
Decreased appetiteMetabolism and nutrition disorders
MyalgiaMusculoskeletal and connective tissue disorders
Abdominal painGastrointestinal disorders
Back painMusculoskeletal and connective tissue disorders
BronchitisInfections and infestations
SyncopeNervous system disorders
Nasal congestionRespiratory, thoracic and mediastinal disorders
PainGeneral disorders
Abdominal pain upperGastrointestinal disorders
InsomniaPsychiatric disorders
HypokalaemiaMetabolism and nutrition disorders
PneumoniaInfections and infestations
Abdominal distensionGastrointestinal disorders
DyspepsiaGastrointestinal disorders
Urinary tract infectionInfections and infestations
AnaemiaBlood and lymphatic system disorders
PyrexiaGeneral disorders
SinusitisInfections and infestations
HypotensionVascular disorders
RashSkin and subcutaneous tissue disorders
EpistaisRespiratory, thoracic and mediastinal disorders

Most-reported serious reactions: Pulmonary Hypertension, Right ventricular failure, Pneumonia, Dyspnoea, Acute kidney injury, Cardiac failure, Syncope, Anaemia.

Data from ClinicalTrials.gov NCT01027949 adverse events section.

Sponsor's own description

This study provided/continued to provide oral treprostinil (UT-15C SR; treprostinil diethanolamine) to eligible subjects who participated in Studies TDE-PH-202, TDE-PH-203, TDE-PH-205, TDE-PH-301, TDE-PH-302, and TDE-PH-308. The study assessed the long term safety of oral treprostinil and the effect of continued treatment with oral treprostinil on exercise capacity after 1 year of treatment.

Publications & conference data

3 peer-reviewed publications reference this trial (live from Europe PMC):

  1. Long-term therapy with oral treprostinil in pulmonary arterial hypertension failed to lead to improvement in important physiologic measures: results from a single center.
    Chin KM, Ruggiero R, Bartolome S, Velez-Martinez M, et al · · 2015 · cited 21× · PMID 26401252 · DOI 10.1086/682224
  2. Treatment of pediatric pulmonary arterial hypertension: A focus on the NO-sGC-cGMP pathway.
    Beghetti M, Gorenflo M, Ivy DD, Moledina S, et al · · 2019 · cited 18× · PMID 31313530 · DOI 10.1002/ppul.24442
  3. EXPRESS: Long term study of oral treprostinil to treat pulmonary arterial hypertension: dosing, tolerability, and pharmacokinetics.
    White RJ, Parikh K, Allen R, Feldman J, et al · · 2019 · cited 1× · PMID 31290359 · DOI 10.1177/2045894019866335

Verify or expand the search:

Other trials of Oral Treprostinil

Trials testing the same drug.

Other recruiting trials for Pulmonary Arterial Hypertension

Currently open trials in the same condition.

Other United Therapeutics trials

Trials by the same sponsor.

Verify against primary sources

Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT01027949.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing