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NCT00890162

A Randomized, Double-Blind, Placebo-Controlled Study of Omalizumab for Idiopathic Anaphylaxis

Completed Phase 2 Results posted Last updated 1 July 2019
What this trial tests

Phase 2 trial testing Epinephrine in Anaphylaxis in 16 participants. Completed in 31 May 2019.

Timeline
27 April 2009
Primary endpoint
31 July 2018
31 May 2019

Quick facts

Lead sponsorNational Institute of Allergy and Infectious Diseases (NIAID)
PhasePhase 2
StatusCompleted
Study typeINTERVENTIONAL
Allocationrandomized
Designparallel
Maskingtriple
Primary purposetreatment
Enrollment16
Start date27 April 2009
Primary completion31 July 2018
Estimated completion31 May 2019
Sites1 location across United States

Drugs / interventions tested

Conditions studied

Sponsor

National Institute of Allergy and Infectious Diseases (NIAID)

Who can join

Adults 18 to 70, any sex, with Anaphylaxis or Hypotension. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Reduction in the Number and Timing of Anaphylactic Events in Subjects With a History of Frequent Idiopathic Anaphylaxis. Primary · 6 months

To determine if treatment with omalizumab over 6 months will produce a reduction in the number and timing of anaphylactic events in subjects with a history of frequent idiopathic anaphylaxis. Ordinal outcome of participants based on number of events in 6 months after baseline and timing of first event. Events were calculated based on detailed event logs maintained by the patients and collected every 2-4 weeks based on injection schedule. Mean percent change in number of events experienced while on study agent for each subject and results presented as a group.

GroupValue95% CI
Omalizumab326 – 57
Placebo6-38 – 50

Adverse events — posted to ClinicalTrials.gov

Time frame: 6 months. Reporting threshold: 0%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Omalizumab
Serious: 3/8 (38%)
Deaths: 0/8
Placebo
Serious: 2/8 (25%)
Deaths: 0/8

Serious adverse events (5 terms)

ReactionSystemOmalizumabPlacebo
HypersensitivityImmune system disorders
Abdominal herniaGastrointestinal disorders
Abdominal painGastrointestinal disorders
Anaphylactic reactionImmune system disorders
NephrolithiasisRenal and urinary disorders
Other adverse events (64 terms — click to expand)

ReactionSystemOmalizumabPlacebo
Injection site painGeneral disorders
HeadacheNervous system disorders
DizzinessCardiac disorders
DyspnoeaCardiac disorders
SyncopeCardiac disorders
HypoglycaemiaEndocrine disorders
DiarrhoeaGastrointestinal disorders
NauseaGastrointestinal disorders
Oropharyngeal painGastrointestinal disorders
FlushingGeneral disorders
Upper respiratory tract infectionInfections and infestations
Back painMusculoskeletal and connective tissue disorders
WheezingRespiratory, thoracic and mediastinal disorders
PruritusSkin and subcutaneous tissue disorders
LymphadenopathyBlood and lymphatic system disorders
Chest discomfortCardiac disorders
Chest painCardiac disorders
Pulmonary congestionCardiac disorders
Sinus bradycardiaCardiac disorders
TachycardiaCardiac disorders
PolydipsiaEndocrine disorders
ConjunctivitisEye disorders
Seasonal allergyEye disorders
Abdominal painGastrointestinal disorders
ConstipationGastrointestinal disorders
DysphagiaGastrointestinal disorders
Oral candidiasisGastrointestinal disorders
Tooth disorderGastrointestinal disorders
VomitingGastrointestinal disorders
ChillsGeneral disorders
Injection site pruritusGeneral disorders
Injection site reactionGeneral disorders
PainGeneral disorders
PyrexiaGeneral disorders
HypoalbuminaemiaHepatobiliary disorders
UrticariaImmune system disorders
BronchitisInfections and infestations
InfectionInfections and infestations
Kidney infectionInfections and infestations
LacerationInjury, poisoning and procedural complications

Most-reported serious reactions: Hypersensitivity, Abdominal hernia, Abdominal pain, Anaphylactic reaction, Nephrolithiasis.

Data from ClinicalTrials.gov NCT00890162 adverse events section.

Sponsor's own description

Background: * Omalizumab is an approved drug for the treatment of asthma by the Food and Drug Administration. * Researchers are now studying this drug in a double-blind placebo-controlled manner to assess efficacy in patients with idiopathic anaphylaxis (recurrent hypersensitive allergic episodes for which a cause is not identified). * The study will improve understanding of the mechanisms involved in anaphylactic reactions as a response to the downregulation (a decrease in the number of receptors on the surface of cells) in mast cell (a resident cell with several types of tissues) activation, and lead to the development of strategies to better prevent or treat anaphylaxis. Objectives: * To determine whether treatment with omalizumab will reduce or prevent episodes of unprovoked anaphylaxis (an acute allergic reaction) in subjects with a history of idiopathic anaphylaxis. * To assess pharmacodynamics (physiological effects of a drug) and identify patients with undiagnosed mastocytosis (rare disorders caused by too many mast cells). * To investigate cellular and molecular mechanisms of signaling and the effect of omalizumab on mast cells or basophils (a cell in the leukocyte family that releases histamine, which affects allergic response) and explore other regulatory pathways that may be involved with modulation of mast cell degranulation. Eligibility: * Patients between 18 and 70 years of age who have been diagnosed with idiopathic anaphylaxis, a diagnosis that is made only after other causes of anaphylaxis have been considered. * Patients with documented anaphylaxis episodes (mild to severe) at least six times within the past 1 year period, at least once within the last 4 months, and with at least one of the following: * Elevated serum tryptase above baseline within 2 hours of the event. * Emergency room visit with documented anaphylaxis without a known cause established by the acute onset of an illness (minutes to several hours) with involvement of the skin, mucosal tissue, or both (generalized hives, itching or flushing, swollen lips-tongue-throat) and at least one of the following: (1) respiratory compromise or gastrointestinal involvement (shortness of breath, wheeze-bronchospasm, throat tightness, low oxygen levels, nausea, vomiting, or abdominal pain); or (2) reduced blood pressure or associated symptoms of end-organ dysfunction (collapse, loss of consciousness, or loss of bladder or bowel control). * Hospitalization for anaphylaxis. * Patients must provide a letter of referral, with copies of pertinent medical history and laboratory tests, from the prospective participant s local physician, and have the ability to give informed consent. * Women with childbearing potential must have a negative pregnancy test, and must agree to practice abstinence or effective birth control from the start of the protocol and for 3 months following the last injection of the study drug. Design: * Participants will undergo a clinical evaluation, blood tests, and a bone marrow biopsy and aspirate. * Participants will be randomized to either drug or placebo and will receive two doses of omalizumab or a matched placebo while hospitalized, followed by continued outpatient therapy, every 2 to 4 weeks, for up to 6 months. * Participants will remain on the assigned regimen for 6 months or until they have experienced new onset of severe adverse event on one occasion within 24 hours of study medication that are related to the study drug, whichever comes first. At that time, the participant will be discontinued from drug administration.

Publications & conference data

No peer-reviewed publications indexed yet for this trial. Completed trials usually publish results within 12-18 months.

Verify or expand the search:

Other trials of Epinephrine

Trials testing the same drug.

Other recruiting trials for Anaphylaxis

Currently open trials in the same condition.

Other National Institute of Allergy and Infectious Diseases (NIAID) trials

Trials by the same sponsor.

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Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing