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NCT00177047

Autologous Transplant for Multiple Myeloma

Completed Phase 2, PHASE3 Results posted Last updated 9 November 2021
What this trial tests

Phase 2, PHASE3 trial testing Stem Cell Transplant in Multiple Myeloma in 363 participants. Completed in 1 August 2020.

Timeline
20 April 2004
Primary endpoint
1 August 2020
1 August 2020

Quick facts

Lead sponsorMasonic Cancer Center, University of Minnesota
PhasePhase 2, PHASE3
StatusCompleted
Study typeINTERVENTIONAL
Allocationna
Designsingle group
Maskingnone
Primary purposetreatment
Enrollment363
Start date20 April 2004
Primary completion1 August 2020
Estimated completion1 August 2020
Sites1 location across United States

Drugs / interventions tested

Conditions studied

Sponsor

Masonic Cancer Center, University of Minnesota

Who can join

Adults 18 to 75, any sex, with Multiple Myeloma. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Number of Participants Achieving a Complete Response Primary · 100 Days post transplant

Myeloma Response Definitions - Using International Uniform Response Criteria: Stringent Complete Response (sCR)requires, plus CR: * Normal free light chain ratio * Absence of clonal cells in bone marrow Complete Response (CR): * Absence of the original monoclonal paraprotein * \<5% plasma cells in a bone marrow aspirate and also on trephine bone biopsy * No increase in size or number of lytic bone lesions * Disappearance of soft tissue plasmacytomas.

GroupValue95% CI
Chemotherapy and Transplant Treatment51
Number of Participants Achieving a Complete Response Primary · 6 months post transplant

Myeloma Response Definitions - Using International Uniform Response Criteria: Stringent Complete Response (sCR)requires, plus CR: * Normal free light chain ratio * Absence of clonal cells in bone marrow Complete Response (CR): * Absence of the original monoclonal paraprotein * \<5% plasma cells in a bone marrow aspirate and also on trephine bone biopsy * No increase in size or number of lytic bone lesions * Disappearance of soft tissue plasmacytomas.

GroupValue95% CI
Chemotherapy and Transplant Treatment99
Number of Participants Achieving a Complete Response Primary · 12 months post transplant

Myeloma Response Definitions - Using International Uniform Response Criteria: Stringent Complete Response (sCR)requires, plus CR: * Normal free light chain ratio * Absence of clonal cells in bone marrow Complete Response (CR): * Absence of the original monoclonal paraprotein * \<5% plasma cells in a bone marrow aspirate and also on trephine bone biopsy * No increase in size or number of lytic bone lesions * Disappearance of soft tissue plasmacytomas.

GroupValue95% CI
Chemotherapy and Transplant Treatment123
Number of Patients With Extended Disease-free Survival Secondary · 36 Months

Extended disease free survival will be defined as percentage of patients surviving more than 36 months without relapse or disease progression.

GroupValue95% CI
Chemotherapy and Transplant Treatment164
Number of Participants With Overall Survival Secondary · 1 year

The percentage of people in a study or treatment group who are alive for a certain period of time after they were diagnosed with or treated for a disease, such as cancer. Also called survival rate.

GroupValue95% CI
Chemotherapy and Transplant Treatment349
Number of Participants With Overall Survival Secondary · 2 years

The percentage of people in a study or treatment group who are alive for a certain period of time after they were diagnosed with or treated for a disease, such as cancer. Also called survival rate.

GroupValue95% CI
Chemotherapy and Transplant Treatment328
Number of Participants With Overall Survival Secondary · 3 years

The percentage of people in a study or treatment group who are alive for a certain period of time after they were diagnosed with or treated for a disease, such as cancer. Also called survival rate.

GroupValue95% CI
Chemotherapy and Transplant Treatment301
Count of Participants Experiencing Transplant Related Mortality Secondary · 1 year

In the field of transplantation, toxicity is high and all deaths without previous relapse or progression are usually considered as related to transplantation.

GroupValue95% CI
Chemotherapy and Transplant Treatment3
Number of Participants Experiencing Incidence of Relapse Secondary · 1 year

The return of disease after its apparent recovery/cessation.

GroupValue95% CI
Chemotherapy and Transplant Treatment69
Number of Participants With Disease Progression Secondary · 1 year

Myeloma Response Definitions - Using International Uniform Response Criteria: Progressive Disease (PD) For patients not in CR or sCR, progressive disease requires one or more of the following: * \>25% increase in the level of the serum monoclonal paraprotein, which must also be an absolute increase of at least 0.5 g/dL. * \>25% increase in 24-hour urine protein electrophoresis, which must also be an absolute increase of at least 200 mg/24 hours. * Absolute increase in the difference between involved and uninvolved FLC levels (absolute increase must be \>10 mg/dl), only in patients without m

GroupValue95% CI
Chemotherapy and Transplant Treatment34
Time to Progression Secondary · 1 year

Mean number of days among patients progressing

GroupValue95% CI
Chemotherapy and Transplant Treatment159.4± 109.8
Time to Relapse Secondary · 1 year

Mean number of days among patients relapsing

GroupValue95% CI
Chemotherapy and Transplant Treatment182.9± 113.5

Adverse events — posted to ClinicalTrials.gov

Time frame: 3 years. Reporting threshold: 0%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Chemotherapy and Transplant Treatment
Serious: 2/363 (1%)
Deaths: 62/363

Serious adverse events (2 terms)

ReactionSystemChemotherapy and Transplan…
M-spike increaseInvestigations
GI bleedingGastrointestinal disorders
Other adverse events (64 terms — click to expand)

ReactionSystemChemotherapy and Transplan…
InfectionInfections and infestations
PneumoniaInfections and infestations
NeuropathyNervous system disorders
ThrombosisBlood and lymphatic system disorders
TachycardiaCardiac disorders
Artrial fibrillationCardiac disorders
GI bleedGastrointestinal disorders
MalnutritionMetabolism and nutrition disorders
bowl obstructionGastrointestinal disorders
Engraftment syndromeGeneral disorders
HypertensionVascular disorders
Acute kidney injuryRenal and urinary disorders
CataractEye disorders
Pericardial effusionCardiac disorders
Blood clotVascular disorders
GoutImmune system disorders
NeurotoxicityNervous system disorders
Physical DeconditioningMusculoskeletal and connective tissue disorders
Pulmonary embolismRespiratory, thoracic and mediastinal disorders
EdemaRenal and urinary disorders
CardiomyopathyCardiac disorders
DiarrheaGastrointestinal disorders
Eye hemorrhageEye disorders
HallucinationsPsychiatric disorders
Hearing lossEar and labyrinth disorders
HerniaInjury, poisoning and procedural complications
HypotensionVascular disorders
IntubationRespiratory, thoracic and mediastinal disorders
Low Ejection fractionCardiac disorders
Pulmonary edemaRespiratory, thoracic and mediastinal disorders
Renal insufficiencyRenal and urinary disorders
SepsisInfections and infestations
ThrombocytopeniaBlood and lymphatic system disorders
AkinesisNervous system disorders
AnorexiaMetabolism and nutrition disorders
AtelectasisRespiratory, thoracic and mediastinal disorders
Chest opacitiesRespiratory, thoracic and mediastinal disorders
CholecystectomySurgical and medical procedures
Congestive heart failureCardiac disorders
CytopeniaBlood and lymphatic system disorders

Most-reported serious reactions: M-spike increase, GI bleeding.

Data from ClinicalTrials.gov NCT00177047 adverse events section.

Sponsor's own description

This is a study of a regimen of melphalan and autologous stem cells for patients with multiple myeloma. We hypothesize that this particular regimen will improve the survival of these patients.

Publications & conference data

1 peer-reviewed publication reference this trial (live from Europe PMC):

  1. Multiple myeloma in the marrow: pathogenesis and treatments.
    Fairfield H, Falank C, Avery L, Reagan MR. · · 2016 · cited 128× · PMID 27002787 · DOI 10.1111/nyas.13038

Verify or expand the search:

Other trials of Stem Cell Transplant

Trials testing the same drug.

Other recruiting trials for Multiple Myeloma

Currently open trials in the same condition.

Other Masonic Cancer Center, University of Minnesota trials

Trials by the same sponsor.

Verify against primary sources

Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT00177047.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing