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NCT00075582

Vincristine, Dactinomycin, and Cyclophosphamide With or Without Radiation Therapy in Treating Patients With Newly Diagnosed Low-Risk Rhabdomyosarcoma

Completed Phase 3 Results posted Last updated 19 November 2021
What this trial tests

Phase 3 trial testing conventional surgery in Adult Rhabdomyosarcoma in 390 participants. Completed in 30 September 2021.

Timeline
4 September 2004
Primary endpoint
13 August 2012
30 September 2021

Quick facts

Lead sponsorChildren's Oncology Group
PhasePhase 3
StatusCompleted
Study typeINTERVENTIONAL
Allocationnon randomized
Designparallel
Maskingnone
Primary purposetreatment
Enrollment390
Start date4 September 2004
Primary completion13 August 2012
Estimated completion30 September 2021
Sites163 locations across New Zealand, Canada, Puerto Rico, Australia, Switzerland, United States

Drugs / interventions tested

Conditions studied

Sponsor

Children's Oncology Group — full company profile →

Who can join

Under 49, any sex, with Adult Rhabdomyosarcoma or Embryonal Childhood Rhabdomyosarcoma. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Percentage of Patients With Low-risk Rhabdomyosarcoma in Subset 1 Failure Free at 5 Years Following Study Entry Primary · From enrollment up to 5 years

Kaplan Meier estimate of failure free survival at 5 years, where failure free survival is defined as the time to relapse, progression, second malignancy, and death whichever occurs first.

GroupValue95% CI
Regimen I (Chemotherapy, Radiotherapy)8782 – 91
Regimen II (Chemotherapy, Radiotherapy, Surgery)6752 – 79
Percentage of Patients With Stage 1, Clinical Group IIB or C (Node Positive) or Stage 2 Failure Free at 5 Years Following Study Entry Primary · From enrollment up to 5 years

Kaplan Meier estimate of failure free survival at 5 years, where failure free survival is defined as the time to relapse, progression, second malignancy, and death whichever occurs first.

GroupValue95% CI
Regimen I (Chemotherapy, Radiotherapy)9072 – 97
Percentage of Patients With Low-risk Rhabdomyosarcoma in Subset 2 Failure Free at 5 Years Following Study Entry Primary · From enrollment up to 5 years

Kaplan Meier estimate of failure free survival at 5 years, where failure free survival is defined as the time to relapse, progression, second malignancy, and death whichever occurs first.

GroupValue95% CI
Regimen II (Chemotherapy, Radiotherapy, Surgery)6752 – 79
Cumulative Incidence of Patients Who Receive Reduced Doses of Radiation Therapy Secondary · From enrollment up to 5 years

The local failure rate will be estimated using cumulative incidence curves.

GroupValue95% CI
Regimen I (Chemotherapy, Radiotherapy)0.0810.046 – 0.116
Regimen II (Chemotherapy, Radiotherapy, Surgery)0.1150.035 – 0.195
Percentage of Patients With Delayed Surgical Procedures Secondary · At 13 weeks after induction

The decision to perform second-look surgery should be based on the physical examination and imaging studies at Week 12 and should only be considered if a reasonable functional and cosmetic result is anticipated.

GroupValue95% CI
Regimen II (Stage I Group III Nonorbit or Stage III Group I/II0.490.34 – 0.64
Cumulative Incidence of Group III Patients Who Received With Reduced Radiotherapy Dose Secondary · From enrollment up to 20 weeks

The local failure rate will be estimated using cumulative incidence curves for Group III patients who received reduced doses of radiation therapy after second look surgical resection.

GroupValue95% CI
Regimen II (Stage I Group III Nonorbit or Stage III Group I/II0

Adverse events — posted to ClinicalTrials.gov

Reporting threshold: 0%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Regimen I (Chemotherapy, Radiotherapy)
Serious: 1/272 (0%)
Deaths:
Regimen II (Chemotherapy, Radiotherapy, Surgery)
Serious: 1/70 (1%)
Deaths:

Serious adverse events (2 terms)

ReactionSystemRegimen I (Chemotherapy, R…Regimen II (Chemotherapy, …
Neutrophil count decreasedInvestigations
White blood cell decreasedInvestigations
Other adverse events (60 terms — click to expand)

ReactionSystemRegimen I (Chemotherapy, R…Regimen II (Chemotherapy, …
Neutrophil count decreasedInvestigations
White blood cell decreasedInvestigations
AnemiaBlood and lymphatic system disorders
Febrile neutropeniaBlood and lymphatic system disorders
Platelet count decreasedInvestigations
Alanine aminotransferase increasedInvestigations
Aspartate aminotransferase increasedInvestigations
VomitingGastrointestinal disorders
FeverGeneral disorders
Infections and infestations - OtherInfections and infestations
HyperglycemiaMetabolism and nutrition disorders
Peripheral motor neuropathyNervous system disorders
Peripheral sensory neuropathyNervous system disorders
ConstipationGastrointestinal disorders
NauseaGastrointestinal disorders
Lymphocyte count decreasedInvestigations
Weight lossInvestigations
Skin and subcutaneous tissue disorders - Other, specifySkin and subcutaneous tissue disorders
Abdominal painGastrointestinal disorders
Mucositis oralGastrointestinal disorders
PainGeneral disorders
Hepatobiliary disorders - OtherHepatobiliary disorders
Catheter related infectionInfections and infestations
Urinary tract infectionInfections and infestations
Blood bilirubin increasedInvestigations
Skin hyperpigmentationSkin and subcutaneous tissue disorders
Disseminated intravascular coagulationBlood and lymphatic system disorders
Sinus tachycardiaCardiac disorders
PhotophobiaEye disorders
Watering eyesEye disorders
DiarrheaGastrointestinal disorders
FlatulenceGastrointestinal disorders
IleusGastrointestinal disorders
Oral painGastrointestinal disorders
Small intestinal obstructionGastrointestinal disorders
Facial painGeneral disorders
FatigueGeneral disorders
Non-cardiac chest painGeneral disorders
Conjunctivitis infectiveInfections and infestations
Rhinitis infectiveInfections and infestations

Most-reported serious reactions: Neutrophil count decreased, White blood cell decreased.

Data from ClinicalTrials.gov NCT00075582 adverse events section.

Sponsor's own description

This phase III trial is studying how well combination chemotherapy and radiation therapy work in treating patients with newly diagnosed low-risk rhabdomyosarcoma. Drugs used in chemotherapy, such as vincristine, dactinomycin, and cyclophosphamide, work in different ways to stop tumor cells from dividing so they stop growing or die. Radiation therapy uses high-energy x-rays to damage tumor cells. Combining chemotherapy with radiation therapy may kill more tumor cells. It is not yet known which treatment regimen is more effective in treating low-risk rhabdomyosarcoma.

Publications & conference data

8 peer-reviewed publications reference this trial (live from Europe PMC):

  1. Refinement of risk stratification for childhood rhabdomyosarcoma using FOXO1 fusion status in addition to established clinical outcome predictors: A report from the Children's Oncology Group.
    Hibbitts E, Chi YY, Hawkins DS, Barr FG, et al · · 2019 · cited 117× · PMID 31456361 · DOI 10.1002/cam4.2504
  2. Inhibition of p53 inhibitors: progress, challenges and perspectives.
    Sanz G, Singh M, Peuget S, Selivanova G. · · 2019 · cited 106× · PMID 31310659 · DOI 10.1093/jmcb/mjz075
  3. Recent advances in understanding and managing pediatric rhabdomyosarcoma.
    Gartrell J, Pappo A. · · 2020 · cited 32× · PMID 32695311 · DOI 10.12688/f1000research.22451.1
  4. Children's Oncology Group's 2013 blueprint for research: radiation oncology.
    Merchant TE, Hodgson D, Laack NN, Wolden S, et al · · 2013 · cited 14× · PMID 23255526 · DOI 10.1002/pbc.24425
  5. Survival of patients with orbital and eyelid rhabdomyosarcoma treated on Children's Oncology Group studies from 1997 to 2013: A report from the Children's Oncology Group.
    Metts J, Xue W, Gao Z, Ermoian R, et al · · 2023 · cited 9× · PMID 36857314 · DOI 10.1002/cncr.34723
  6. Prognostic factors of pediatric pelvic and genitourinary rhabdomyosarcoma: An analysis based on SEER database.
    Wu J, Shou X, Cai J, Mao J, et al · · 2022 · cited 5× · PMID 36132132 · DOI 10.3389/fonc.2022.992738
  7. Patients with completely resected nongenitourinary low-risk embryonal rhabdomyosarcoma are candidates for reduced duration low-intensity chemotherapy.
    Bisogno G, Fuchs J, Dasgupta R, Ferrari A, et al · · 2022 · cited 4× · PMID 36250420 · DOI 10.1002/cncr.34497
  8. Extremity rhabdomyosarcoma in children, adolescents and young adults: A report from Children's Oncology Group trials.
    Oberoi S, Xue W, Qumseya A, Scharschmidt T, et al · · 2025 · cited 3× · PMID 40464368 · DOI 10.1002/cncr.35929

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Trials by the same sponsor.

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Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT00075582.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing