Iduronate-2-sulfatase — Drug Target
All drugs that target Iduronate-2-sulfatase — marketed and clinical-stage. Includes 1 drug classes acting on this target.
Drug classes
Phase 3 pipeline (1)
- JR-141 or Idursulfase · JCR Pharmaceuticals Co., Ltd. · Enzyme replacement therapy · Rare genetic disease / Lysosomal storage disorder
JR-141 is a recombinant idursulfase enzyme that replaces deficient iduronate-2-sulfatase to break down glycosaminoglycans in Hunter syndrome.