DMPK mRNA — Drug Target

All drugs that target DMPK mRNA — marketed and clinical-stage. Includes 1 drug classes acting on this target.

Drug classes

Antisense oligonucleotide

Phase 3 pipeline (1)

• SRP-9003 · Sarepta Therapeutics, Inc. · Antisense oligonucleotide · Neuromuscular/Genetic Disorders
  SRP-9003 is an antisense oligonucleotide that reduces production of DMPK protein by targeting mutant DMPK mRNA in myotonic dystrophy type 1.