What drugs target ABCD1 gene?

1+ drugs target ABCD1 gene, including .

What drug classes act on ABCD1 gene?

Drug classes acting on ABCD1 gene include Gene therapy.

1 drugs 1 in Phase 3

All drugs that target ABCD1 gene — marketed and clinical-stage. Includes 1 drug classes acting on this target.

EB-101 · Abeona Therapeutics, Inc · Gene therapy · Neurology
EB-101 is a gene therapy that delivers a functional copy of the ABCD1 gene to restore adrenoleukodystrophy protein function in patients with cerebral adrenoleukodystrophy.