What drugs target ABCA3 gene?

1+ drugs target ABCA3 gene, including .

What drug classes act on ABCA3 gene?

Drug classes acting on ABCA3 gene include Gene therapy.

1 drugs 1 in Phase 3

All drugs that target ABCA3 gene — marketed and clinical-stage. Includes 1 drug classes acting on this target.

MDR-101 · Medeor Therapeutics, Inc. · Gene therapy · Pulmonology / Rare Genetic Lung Disease
MDR-101 is a gene therapy that delivers a functional copy of the ABCA3 gene to restore surfactant production in patients with ABCA3-deficient interstitial lung disease.