CN Patent
CN121358748A — 包含糖的寡核苷酸递送配体
Assigned to Darui Biomedical Technology Shanghai Co ltd · Expires 2026-01-16 · 0y expired
What this patent protects
提供式(I)化合物,或其药学上可接受的盐、互变异构体或立体异构体。所述式(I)化合物包含在核苷酸内部,或者在5′端和/或3′端,用于将双链RNA递送至肝外组织,例如中枢神经系统或眼部。还提供包含式(I)化合物的寡核苷酸、双链RNA、载体、细胞、药物组合物和试剂盒。
USPTO Abstract
提供式(I)化合物,或其药学上可接受的盐、互变异构体或立体异构体。所述式(I)化合物包含在核苷酸内部,或者在5′端和/或3′端,用于将双链RNA递送至肝外组织,例如中枢神经系统或眼部。还提供包含式(I)化合物的寡核苷酸、双链RNA、载体、细胞、药物组合物和试剂盒。
Drugs covered by this patent
Bibliographic data sourced from FDA Orange Book + USPTO public records. Plain-English summary generated by AI grounded in source text. Patent term extensions (PTR, SPC, pediatric) may shift the effective expiry. Not legal advice.
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