CN Patent

CN121358748A — 包含糖的寡核苷酸递送配体

Assigned to Darui Biomedical Technology Shanghai Co ltd · Expires 2026-01-16 · 0y expired

What this patent protects

提供式(I)化合物,或其药学上可接受的盐、互变异构体或立体异构体。所述式(I)化合物包含在核苷酸内部,或者在5′端和/或3′端,用于将双链RNA递送至肝外组织,例如中枢神经系统或眼部。还提供包含式(I)化合物的寡核苷酸、双链RNA、载体、细胞、药物组合物和试剂盒。

USPTO Abstract

提供式(I)化合物,或其药学上可接受的盐、互变异构体或立体异构体。所述式(I)化合物包含在核苷酸内部,或者在5′端和/或3′端,用于将双链RNA递送至肝外组织,例如中枢神经系统或眼部。还提供包含式(I)化合物的寡核苷酸、双链RNA、载体、细胞、药物组合物和试剂盒。

Drugs covered by this patent

Patent Metadata

Patent number
CN121358748A
Jurisdiction
CN
Classification
Expires
2026-01-16
Drug substance claim
No
Drug product claim
No
Assignee
Darui Biomedical Technology Shanghai Co ltd
Source
FDA Orange Book + USPTO grounding via Google Patents

Bibliographic data sourced from FDA Orange Book + USPTO public records. Plain-English summary generated by AI grounded in source text. Patent term extensions (PTR, SPC, pediatric) may shift the effective expiry. Not legal advice.

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