CN Patent
CN121318878A — 基于“古德”缓冲液的阳离子脂质
Assigned to Translation Bio Co · Expires 2026-01-13 · 0y expired
What this patent protects
本发明部分提供了式(I)和其子式的第二代基于“古德”缓冲液的阳离子脂质:(I),或其药学上可接受的盐。本文提供的化合物可例如作为脂质体递送媒介物的组分用于mRNA和所编码蛋白质的递送和表达,并且因此可用于治疗各种疾病、障碍和病症,如与一种或多种蛋白质的缺乏相关的那些。
USPTO Abstract
本发明部分提供了式(I)和其子式的第二代基于“古德”缓冲液的阳离子脂质:(I),或其药学上可接受的盐。本文提供的化合物可例如作为脂质体递送媒介物的组分用于mRNA和所编码蛋白质的递送和表达,并且因此可用于治疗各种疾病、障碍和病症,如与一种或多种蛋白质的缺乏相关的那些。
Drugs covered by this patent
- Onpattro (PATISIRAN SODIUM) · Alnylam Pharmaceuticals
Bibliographic data sourced from FDA Orange Book + USPTO public records. Plain-English summary generated by AI grounded in source text. Patent term extensions (PTR, SPC, pediatric) may shift the effective expiry. Not legal advice.
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