CN Patent
CN120272480A — 用于治疗与pcsk9相关疾病的靶向寡核苷酸
Assigned to Beijing Anlong Biomedical Co ltd · Expires 2025-07-08 · 1y expired
What this patent protects
本公开涉及用于治疗与PCSK9相关疾病的靶向寡核苷酸,所述靶向寡核苷酸包含反义链,所述反义链具有如SEQ ID NO:53‑106中任一所示的序列或其片段、或所述序列或其片段的修饰序列。所述靶向寡核苷酸显著抑制中PCSK9基因表达水平,降低血液中低密度脂蛋白胆固醇(LDL‑C)水平,表现出良好的降脂效果。
USPTO Abstract
本公开涉及用于治疗与PCSK9相关疾病的靶向寡核苷酸,所述靶向寡核苷酸包含反义链,所述反义链具有如SEQ ID NO:53‑106中任一所示的序列或其片段、或所述序列或其片段的修饰序列。所述靶向寡核苷酸显著抑制中PCSK9基因表达水平,降低血液中低密度脂蛋白胆固醇(LDL‑C)水平,表现出良好的降脂效果。
Drugs covered by this patent
Bibliographic data sourced from FDA Orange Book + USPTO public records. Plain-English summary generated by AI grounded in source text. Patent term extensions (PTR, SPC, pediatric) may shift the effective expiry. Not legal advice.
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