CN118717992B — 补体因子c3作为结晶样视网膜色素变性治疗靶点的应用
Assigned to Huazhong University of Science and Technology · Expires 2025-01-28 · 1y expired
What this patent protects
本发明属于眼科疾病治疗技术领域,尤其涉及补体因子C3作为结晶样视网膜色素变性治疗靶点的应用。本发明首次提出补体因子C3作为结晶样视网膜色素变性的治疗靶点,通过抑制补体因子C3的功能,可显著改善结晶样视网膜色素变性细胞和斑马鱼模型的脂质代谢紊乱的情况,减缓脂滴的累积,为治疗结晶样视网膜色素变性提供了有利证据。而且本发明的治疗方法简单,成本较低,与基因疗法和细胞治疗等相比具有显著优势。
USPTO Abstract
本发明属于眼科疾病治疗技术领域,尤其涉及补体因子C3作为结晶样视网膜色素变性治疗靶点的应用。本发明首次提出补体因子C3作为结晶样视网膜色素变性的治疗靶点,通过抑制补体因子C3的功能,可显著改善结晶样视网膜色素变性细胞和斑马鱼模型的脂质代谢紊乱的情况,减缓脂滴的累积,为治疗结晶样视网膜色素变性提供了有利证据。而且本发明的治疗方法简单,成本较低,与基因疗法和细胞治疗等相比具有显著优势。
Drugs covered by this patent
- Lotemax (LOTEPREDNOL ETABONATE) · Bausch Health
Bibliographic data sourced from FDA Orange Book + USPTO public records. Plain-English summary generated by AI grounded in source text. Patent term extensions (PTR, SPC, pediatric) may shift the effective expiry. Not legal advice.
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