CN Patent
CN117210468B — 靶向调控PCSK9基因表达的siRNA及其应用
Assigned to Hangzhou Tianlong Pharmaceutical Co Ltd · Expires 2024-02-20 · 2y expired
What this patent protects
本公开涉及靶向调控PCSK9基因表达的siRNA及其应用。实验结果显示,一些交替修饰和特定模板修饰的寡核苷酸序列,能够显著抑制PCSK9表达,可用于开发治疗PCSK9相关疾病的药物。
USPTO Abstract
本公开涉及靶向调控PCSK9基因表达的siRNA及其应用。实验结果显示,一些交替修饰和特定模板修饰的寡核苷酸序列,能够显著抑制PCSK9表达,可用于开发治疗PCSK9相关疾病的药物。
Drugs covered by this patent
Bibliographic data sourced from FDA Orange Book + USPTO public records. Plain-English summary generated by AI grounded in source text. Patent term extensions (PTR, SPC, pediatric) may shift the effective expiry. Not legal advice.
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