CN Patent
CN117062911A — 肌萎缩性脊髓侧索硬化症的治疗
Assigned to Bojian Massachusetts Co ltd · Expires 2023-11-14 · 3y expired
What this patent protects
本公开提供了神经丝轻链水平在选择具有过氧化物歧化酶1(SOD1)基因的突变的受试者以用SOD1靶向反义寡核苷酸或其盐进行治疗中的用途。所述公开的方法可用于治疗肌萎缩性脊髓侧索硬化症,包括临床上症状发生前肌萎缩性脊髓侧索硬化症。
USPTO Abstract
本公开提供了神经丝轻链水平在选择具有过氧化物歧化酶1(SOD1)基因的突变的受试者以用SOD1靶向反义寡核苷酸或其盐进行治疗中的用途。所述公开的方法可用于治疗肌萎缩性脊髓侧索硬化症,包括临床上症状发生前肌萎缩性脊髓侧索硬化症。
Drugs covered by this patent
- Qalsody (TOFERSEN) · Biogen Ma
Bibliographic data sourced from FDA Orange Book + USPTO public records. Plain-English summary generated by AI grounded in source text. Patent term extensions (PTR, SPC, pediatric) may shift the effective expiry. Not legal advice.
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