CN Patent
CN116096886A — 用于调节叉头框p3(foxp3)基因表达的组合物和方法
Assigned to Omega Therapeutics Inc · Expires 2023-05-09 · 3y expired
What this patent protects
本发明提供用于通过靶向FOXP3表达控制区来调节叉头框P3(FOXP3)基因的表达(例如,增加或降低表达)的试剂和组合物,以及其用于治疗FOXP3相关病症(例如自身免疫性疾病,如IPEX综合征)的使用方法。
USPTO Abstract
本发明提供用于通过靶向FOXP3表达控制区来调节叉头框P3(FOXP3)基因的表达(例如,增加或降低表达)的试剂和组合物,以及其用于治疗FOXP3相关病症(例如自身免疫性疾病,如IPEX综合征)的使用方法。
Drugs covered by this patent
- Onpattro (PATISIRAN SODIUM) · Alnylam Pharmaceuticals
Bibliographic data sourced from FDA Orange Book + USPTO public records. Plain-English summary generated by AI grounded in source text. Patent term extensions (PTR, SPC, pediatric) may shift the effective expiry. Not legal advice.
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