CN Patent
CN115516092B — 血管生成素样3(ANGPTL3)的siRNA及其用途
Assigned to Eddingpharm (Zhuhai) Co.,Ltd. · Expires 2025-05-16 · 1y expired
What this patent protects
提供一种血管生成素样3(ANGPTL3)的siRNA及其用途。通过设计合适的特异性小干扰RNA序列以及siRNA缀合物,靶向ANGPTL3,通过降解细胞中ANGPTL3基因的转录物,从而降低ANGPTL3蛋白表达量,所述的siRNA可用于预防和/或治疗血脂异常疾病。
USPTO Abstract
提供一种血管生成素样3(ANGPTL3)的siRNA及其用途。通过设计合适的特异性小干扰RNA序列以及siRNA缀合物,靶向ANGPTL3,通过降解细胞中ANGPTL3基因的转录物,从而降低ANGPTL3蛋白表达量,所述的siRNA可用于预防和/或治疗血脂异常疾病。
Drugs covered by this patent
Bibliographic data sourced from FDA Orange Book + USPTO public records. Plain-English summary generated by AI grounded in source text. Patent term extensions (PTR, SPC, pediatric) may shift the effective expiry. Not legal advice.
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