CN Patent

CN115227710A — 用于在对象中调节smn2剪接的组合物和方法

Assigned to Bojian Massachusetts Co ltd · Expires 2022-10-25 · 4y expired

What this patent protects

本发明公开了用于调节对象中的SMN2mRNA剪接的化合物、组合物和方法。还提供了所公开的化合物和组合物用于生产药物的用途,所述药物用于治疗疾病和病症,包括脊髓性肌萎缩症。

USPTO Abstract

本发明公开了用于调节对象中的SMN2mRNA剪接的化合物、组合物和方法。还提供了所公开的化合物和组合物用于生产药物的用途,所述药物用于治疗疾病和病症,包括脊髓性肌萎缩症。

Drugs covered by this patent

Patent Metadata

Patent number
CN115227710A
Jurisdiction
CN
Classification
Expires
2022-10-25
Drug substance claim
No
Drug product claim
No
Assignee
Bojian Massachusetts Co ltd
Source
FDA Orange Book + USPTO grounding via Google Patents

Bibliographic data sourced from FDA Orange Book + USPTO public records. Plain-English summary generated by AI grounded in source text. Patent term extensions (PTR, SPC, pediatric) may shift the effective expiry. Not legal advice.

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