CN Patent
CN115227710A — 用于在对象中调节smn2剪接的组合物和方法
Assigned to Bojian Massachusetts Co ltd · Expires 2022-10-25 · 4y expired
What this patent protects
本发明公开了用于调节对象中的SMN2mRNA剪接的化合物、组合物和方法。还提供了所公开的化合物和组合物用于生产药物的用途,所述药物用于治疗疾病和病症,包括脊髓性肌萎缩症。
USPTO Abstract
本发明公开了用于调节对象中的SMN2mRNA剪接的化合物、组合物和方法。还提供了所公开的化合物和组合物用于生产药物的用途,所述药物用于治疗疾病和病症,包括脊髓性肌萎缩症。
Drugs covered by this patent
Bibliographic data sourced from FDA Orange Book + USPTO public records. Plain-English summary generated by AI grounded in source text. Patent term extensions (PTR, SPC, pediatric) may shift the effective expiry. Not legal advice.
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