CN Patent
CN114729376A — 用于调节肝细胞核因子4α(HNF4α)基因表达的组合物和方法
Assigned to Omega Therapeutics Inc · Expires 2022-07-08 · 4y expired
What this patent protects
本发明提供用于通过靶向HNF4α表达控制区来调节肝细胞核因子4α(HNF4α)基因的表达(例如增加或降低的表达)的试剂和组合物及其用于治疗HNF4α相关病症(例如肝硬化)的使用方法。
USPTO Abstract
本发明提供用于通过靶向HNF4α表达控制区来调节肝细胞核因子4α(HNF4α)基因的表达(例如增加或降低的表达)的试剂和组合物及其用于治疗HNF4α相关病症(例如肝硬化)的使用方法。
Drugs covered by this patent
- Onpattro (PATISIRAN SODIUM) · Alnylam Pharmaceuticals
Bibliographic data sourced from FDA Orange Book + USPTO public records. Plain-English summary generated by AI grounded in source text. Patent term extensions (PTR, SPC, pediatric) may shift the effective expiry. Not legal advice.
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