CN Patent
CN112437767B — 硫酯阳离子脂质
Assigned to Translate Bio Inc · Expires 2023-10-27 · 3y expired
What this patent protects
本发明公开了阳离子脂质,所述阳离子脂质是式(I)、(II)、(III)、(IV)、(V)或(VI)的化合物。本文提供的阳离子脂质可用于递送和表达mRNA及所编码的蛋白质,例如作为脂质体递送媒介物的组分,并因此可用于治疗各种疾病、病症和病状,诸如与一种或多种蛋白质的缺乏相关的那些。
USPTO Abstract
本发明公开了阳离子脂质,所述阳离子脂质是式(I)、(II)、(III)、(IV)、(V)或(VI)的化合物。本文提供的阳离子脂质可用于递送和表达mRNA及所编码的蛋白质,例如作为脂质体递送媒介物的组分,并因此可用于治疗各种疾病、病症和病状,诸如与一种或多种蛋白质的缺乏相关的那些。
Drugs covered by this patent
- Onpattro (PATISIRAN SODIUM) · Alnylam Pharmaceuticals
Bibliographic data sourced from FDA Orange Book + USPTO public records. Plain-English summary generated by AI grounded in source text. Patent term extensions (PTR, SPC, pediatric) may shift the effective expiry. Not legal advice.
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