CN Patent
CN112251436A — 治疗杜兴型肌营养不良症和贝克型肌营养不良症的具有改善特性的rna调节性寡核苷酸
Assigned to Biomarin Technologies BV · Expires 2021-01-22 · 5y expired
What this patent protects
本发明涉及治疗杜兴型肌营养不良症和贝克型肌营养不良症的具有改善特性的RNA调节性寡核苷酸。具体地,本发明提供改善的寡核苷酸和其用于治疗、缓解、预防和/或延迟DMD或BMD的应用。
USPTO Abstract
本发明涉及治疗杜兴型肌营养不良症和贝克型肌营养不良症的具有改善特性的RNA调节性寡核苷酸。具体地,本发明提供改善的寡核苷酸和其用于治疗、缓解、预防和/或延迟DMD或BMD的应用。
Drugs covered by this patent
- Amondys 45 (CASIMERSEN) · Sarepta
Bibliographic data sourced from FDA Orange Book + USPTO public records. Plain-English summary generated by AI grounded in source text. Patent term extensions (PTR, SPC, pediatric) may shift the effective expiry. Not legal advice.
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