CN Patent
CN109563511A — 用于递送信使rna的组合物和方法
Assigned to Abt J Biopharmaceutical Co · Expires 2019-04-02 · 7y expired
What this patent protects
本发明提供了包含包封在脂质颗粒内的核酸分子例如mRNA分子的组合物。所述组合物可用于例如将所述mRNA分子引入人类受试者体内,在所述人类受试者体内,所述mRNA分子被翻译以生成用于改善疾病的一种或多种症状的多肽。
USPTO Abstract
本发明提供了包含包封在脂质颗粒内的核酸分子例如mRNA分子的组合物。所述组合物可用于例如将所述mRNA分子引入人类受试者体内,在所述人类受试者体内,所述mRNA分子被翻译以生成用于改善疾病的一种或多种症状的多肽。
Drugs covered by this patent
- Onpattro (PATISIRAN SODIUM) · Alnylam Pharmaceuticals
Bibliographic data sourced from FDA Orange Book + USPTO public records. Plain-English summary generated by AI grounded in source text. Patent term extensions (PTR, SPC, pediatric) may shift the effective expiry. Not legal advice.
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