CN Patent
CN106103717A — 用于调节共济失调蛋白2表达的组合物
Assigned to Ionis Pharmaceuticals Inc · Expires 2016-11-09 · 10y expired
What this patent protects
本文公开了用于降低共济失调蛋白2mRNA和蛋白质表达的反义化合物和方法。所述方法、化合物和组合物可用于治疗、预防或改善共济失调蛋白2相关疾病、病症或病状。所述共济失调蛋白2相关疾病包括脊髓小脑性共济失调2型(SCA2)、肌萎缩性侧索硬化症(ALS)和帕金森症。
USPTO Abstract
本文公开了用于降低共济失调蛋白2mRNA和蛋白质表达的反义化合物和方法。所述方法、化合物和组合物可用于治疗、预防或改善共济失调蛋白2相关疾病、病症或病状。所述共济失调蛋白2相关疾病包括脊髓小脑性共济失调2型(SCA2)、肌萎缩性侧索硬化症(ALS)和帕金森症。
Drugs covered by this patent
Bibliographic data sourced from FDA Orange Book + USPTO public records. Plain-English summary generated by AI grounded in source text. Patent term extensions (PTR, SPC, pediatric) may shift the effective expiry. Not legal advice.
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