CN Patent

CN105307723A — 改进的用于治疗肌营养不良的组合物

Assigned to Sarepta Therapeutics Inc · Expires 2016-02-03 · 10y expired

What this patent protects

描述了通过施用反义分子来治疗肌营养不良的改进的组合物和方法,所述反义分子能够结合人肌养蛋白基因中的选定靶位以诱导外显子跳跃。

USPTO Abstract

描述了通过施用反义分子来治疗肌营养不良的改进的组合物和方法,所述反义分子能够结合人肌养蛋白基因中的选定靶位以诱导外显子跳跃。

Drugs covered by this patent

Patent Metadata

Patent number
CN105307723A
Jurisdiction
CN
Classification
Expires
2016-02-03
Drug substance claim
No
Drug product claim
No
Assignee
Sarepta Therapeutics Inc
Source
FDA Orange Book + USPTO grounding via Google Patents

Bibliographic data sourced from FDA Orange Book + USPTO public records. Plain-English summary generated by AI grounded in source text. Patent term extensions (PTR, SPC, pediatric) may shift the effective expiry. Not legal advice.

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