CN Patent

CN102665731A — 用于在对象中调节smn2剪接的组合物和方法

Assigned to Cold Spring Harbor Laboratory · Expires 2012-09-12 · 14y expired

What this patent protects

本发明公开了用于调节对象中的SMN2mRNA剪接的化合物、组合物和方法。还提供了所公开的化合物和组合物用于生产药物的用途,所述药物用于治疗疾病和病症,包括脊髓性肌萎缩症。

USPTO Abstract

本发明公开了用于调节对象中的SMN2mRNA剪接的化合物、组合物和方法。还提供了所公开的化合物和组合物用于生产药物的用途,所述药物用于治疗疾病和病症,包括脊髓性肌萎缩症。

Drugs covered by this patent

Patent Metadata

Patent number
CN102665731A
Jurisdiction
CN
Classification
Expires
2012-09-12
Drug substance claim
No
Drug product claim
No
Assignee
Cold Spring Harbor Laboratory
Source
FDA Orange Book + USPTO grounding via Google Patents

Bibliographic data sourced from FDA Orange Book + USPTO public records. Plain-English summary generated by AI grounded in source text. Patent term extensions (PTR, SPC, pediatric) may shift the effective expiry. Not legal advice.

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