CA3039673A1 — Methods and compositions for the treatment of fabry disease
Assigned to Sangamo Therapeutics Inc · Expires 2018-04-26 · 8y expired
What this patent protects
The disclosure provides nucleases and methods of using these nucleases for inserting a sequence encoding a therapeutic alpha galactosidase A (alpha-Gal A) protein such as an enzyme into a cell, thereby providing proteins or cell therapeutics for treatment and/or prevention of Fab…
USPTO Abstract
The disclosure provides nucleases and methods of using these nucleases for inserting a sequence encoding a therapeutic alpha galactosidase A (alpha-Gal A) protein such as an enzyme into a cell, thereby providing proteins or cell therapeutics for treatment and/or prevention of Fabry disease. Further provided are compositions for expressing at least one alpha-Gal A protein.
Drugs covered by this patent
Bibliographic data sourced from FDA Orange Book + USPTO public records. Plain-English summary generated by AI grounded in source text. Patent term extensions (PTR, SPC, pediatric) may shift the effective expiry. Not legal advice.
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