CA Patent

CA3029772A1 — Pre-mrna splice switching or modulating oligonucleotides comprising bicyclic scaffold moieties, with improved characteristics for the treatment of genetic disorders

Assigned to Biomarin Technologies BV · Expires 2018-01-11 · 8y expired

What this patent protects

The current invention provides antisense splice-switching oligonucleotides with improved characteristics that enhance clinical applicability for treating, ameliorating, preventing, and/or delaying neuromuscular disorders, such as DMD.

USPTO Abstract

The current invention provides antisense splice-switching oligonucleotides with improved characteristics that enhance clinical applicability for treating, ameliorating, preventing, and/or delaying neuromuscular disorders, such as DMD.

Drugs covered by this patent

Patent Metadata

Patent number
CA3029772A1
Jurisdiction
CA
Classification
Expires
2018-01-11
Drug substance claim
No
Drug product claim
No
Assignee
Biomarin Technologies BV
Source
FDA Orange Book + USPTO grounding via Google Patents

Bibliographic data sourced from FDA Orange Book + USPTO public records. Plain-English summary generated by AI grounded in source text. Patent term extensions (PTR, SPC, pediatric) may shift the effective expiry. Not legal advice.

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