AU2023403208A1 — Modulation of syngap1 gene transcription using antisense oligonucleotides targeting regulatory rnas
Assigned to Camp4 Therapeutics Corp · Expires 2025-06-19 · 1y expired
What this patent protects
Described herein are methods of modulating SYNGAP1 gene transcription using antisense oligonucleotides (ASOs) targeting regulatory RNAs, such as promoter-associated RNAs, enhancer RNAs, and natural antisense transcripts (NATs). These methods are useful for increasing expression o…
USPTO Abstract
Described herein are methods of modulating SYNGAP1 gene transcription using antisense oligonucleotides (ASOs) targeting regulatory RNAs, such as promoter-associated RNAs, enhancer RNAs, and natural antisense transcripts (NATs). These methods are useful for increasing expression of SYNGAP1 mRNA and protein, thereby treating diseases associated with SYNGAP1 mutations.
Drugs covered by this patent
- Onpattro (PATISIRAN SODIUM) · Alnylam Pharmaceuticals
Bibliographic data sourced from FDA Orange Book + USPTO public records. Plain-English summary generated by AI grounded in source text. Patent term extensions (PTR, SPC, pediatric) may shift the effective expiry. Not legal advice.
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