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Vitamin B12 (Cyanocobalamin)

University of Aarhus · FDA-approved active Small molecule

Vitamin B12 (cyanocobalamin) acts as a coenzyme essential for DNA synthesis, myelin formation, and cellular metabolism.

Vitamin B12 (cyanocobalamin) acts as a coenzyme essential for DNA synthesis, myelin formation, and cellular metabolism. Used for Vitamin B12 deficiency anemia, Pernicious anemia, B12 deficiency due to malabsorption or dietary insufficiency.

At a glance

Generic nameVitamin B12 (Cyanocobalamin)
Also known asB12 Ankermann®
SponsorUniversity of Aarhus
Drug classVitamin / Essential nutrient
TargetMethionine synthase; methylmalonyl-CoA mutase
ModalitySmall molecule
Therapeutic areaHematology; Neurology; Nutritional deficiency
PhaseFDA-approved

Mechanism of action

Cyanocobalamin is converted to its active forms (methylcobalamin and adenosylcobalamin) in the body, where it serves as a critical cofactor for methionine synthase and methylmalonyl-CoA mutase enzymes. These enzymes are required for proper DNA replication, red blood cell formation, and nervous system function. B12 deficiency leads to megaloblastic anemia and neurological complications that are reversed by supplementation.

Approved indications

Common side effects

Key clinical trials

Primary sources

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SourceUsed for
ClinicalTrials.govTrial enrolment, design, endpoints, results

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