EMA — authorised 30 June 2025
- Application: EMEA/H/C/006382
- Marketing authorisation holder: Vertex Pharmaceuticals (Ireland) Limited
- Local brand name: Alyftrek
- Indication: Alyftrek tablets are indicated for the treatment of cystic fibrosis (CF) in people aged 6 years and older who have at least one non-Class I mutation in the cystic fibrosis transmembrane conductance regulator (CFTR) gene (see sections 4.2 and 5.1).
- Pathway: orphan
- Status: approved
The European Medicines Agency (EMA) has granted marketing authorisation for Alyftrek tablets, developed by Vertex Pharmaceuticals (Ireland) Limited. Alyftrek is indicated for the treatment of cystic fibrosis (CF) in people aged 6 years and older who have at least one non-Class I mutation in the cystic fibrosis transmembrane conductance regulator (CFTR) gene. This approval was granted under the orphan designation, which is reserved for medicines that treat rare diseases.