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Tafamidis Pill

Peking University Third Hospital · FDA-approved active Small molecule ✓ Verified May 2026 Quality 2/100

Tafamidis Pill is a Small molecule drug developed by Peking University Third Hospital. It is currently FDA-approved.

Tafamidis is a small molecule that stabilizes transthyretin, a protein associated with Transthyretin Amyloidosis. It is used to treat Transthyretin Amyloidosis, specifically Transthyretin Amyloid Polyneuropathy, as indicated by clinical trials.

At a glance

Generic nameTafamidis Pill
SponsorPeking University Third Hospital
ModalitySmall molecule
PhaseFDA-approved

Approved indications

No approved indications tracked.

Common side effects

No common side effects on file.

Key clinical trials

Primary sources

Every claim on this page is sourced from regulatory or scientific primary sources. See our editorial policy for full methodology.

SourceUsed for
ClinicalTrials.govTrial enrolment, design, endpoints, results

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Frequently asked questions about Tafamidis Pill

What is Tafamidis Pill?

Tafamidis Pill is a Small molecule drug developed by Peking University Third Hospital.

Who makes Tafamidis Pill?

Tafamidis Pill is developed and marketed by Peking University Third Hospital (see full Peking University Third Hospital pipeline at /company/peking-university-third-hospital).

What development phase is Tafamidis Pill in?

Tafamidis Pill is FDA-approved (marketed).

Related

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing