Last reviewed · How we verify

Syfovre™

Hoffmann-La Roche · FDA-approved active Small molecule

Syfovre is an anti-VEGF aptamer that binds and inhibits vascular endothelial growth factor (VEGF), reducing abnormal blood vessel growth and leakage in the retina.

Syfovre is an anti-VEGF aptamer that binds and inhibits vascular endothelial growth factor (VEGF), reducing abnormal blood vessel growth and leakage in the retina. Used for Geographic atrophy secondary to age-related macular degeneration (AMD).

At a glance

Generic nameSyfovre™
Also known asPegcetacoplan injection
SponsorHoffmann-La Roche
Drug classAnti-VEGF aptamer
TargetVEGF-A
ModalitySmall molecule
Therapeutic areaOphthalmology
PhaseFDA-approved

Mechanism of action

Syfovre (pegcetacoplan) is a 40-nucleotide RNA aptamer that directly binds to VEGF-A, preventing its interaction with VEGF receptors on endothelial cells. By blocking VEGF signaling, it reduces pathological neovascularization and vascular permeability in the eye. It is administered via intravitreal injection directly into the eye to achieve high local concentrations while minimizing systemic exposure.

Approved indications

Common side effects

Key clinical trials

Primary sources

Every claim on this page is sourced from regulatory or scientific primary sources. See our editorial policy for full methodology.

SourceUsed for
ClinicalTrials.govTrial enrolment, design, endpoints, results

Competitive intelligence

For the full competitive landscape — auto-detected comparators, recent regulatory actions across the set, upcoming PDUFA, patent timeline, sponsor landscape: