Last reviewed · How we verify
sapropterin dihydrochloride, 6R-BH4, tetrahydrobiopterin
sapropterin dihydrochloride, 6R-BH4, tetrahydrobiopterin is a Small molecule drug developed by BioMarin Pharmaceutical. It is currently in Phase 3 development.
At a glance
| Generic name | sapropterin dihydrochloride, 6R-BH4, tetrahydrobiopterin |
|---|---|
| Sponsor | BioMarin Pharmaceutical |
| Modality | Small molecule |
| Phase | Phase 3 |
Approved indications
Common side effects
Key clinical trials
- Evaluation of BH4 Responsiveness in Our PKU Patients (PHASE1)
- Exercise and NO in HFrEF (EARLY_PHASE1)
- Novel Approaches for Improving Vascular Function in Veterans With HFpEF (PHASE1)
- Study of Kuvan Treatment in Adults With GTPCH Deficiency (PHASE1, PHASE2)
- Neurovascular Transduction During Exercise in Chronic Kidney Disease (PHASE2)
- Effects of Tetrahydrobiopterin (BH4) on Leg Blood Flow and Exercise Capacity in Patients With Peripheral Artery Disease (PHASE4)
- O2 Transport and Utilization in Health and Lung Disease (PHASE1)
- The Effectiveness of Kuvan in Amish PKU Patients (PHASE4)
Primary sources
Every claim on this page is sourced from regulatory or scientific primary sources. See our editorial policy for full methodology.
| Source | Used for |
|---|---|
| ClinicalTrials.gov | Trial enrolment, design, endpoints, results |
Competitive intelligence
For the full competitive landscape — auto-detected comparators, recent regulatory actions across the set, upcoming PDUFA, patent timeline, sponsor landscape:
- sapropterin dihydrochloride, 6R-BH4, tetrahydrobiopterin CI brief — competitive landscape report
- sapropterin dihydrochloride, 6R-BH4, tetrahydrobiopterin updates RSS · CI watch RSS
- BioMarin Pharmaceutical portfolio CI
Frequently asked questions about sapropterin dihydrochloride, 6R-BH4, tetrahydrobiopterin
What is sapropterin dihydrochloride, 6R-BH4, tetrahydrobiopterin?
sapropterin dihydrochloride, 6R-BH4, tetrahydrobiopterin is a Small molecule drug developed by BioMarin Pharmaceutical.
Who makes sapropterin dihydrochloride, 6R-BH4, tetrahydrobiopterin?
sapropterin dihydrochloride, 6R-BH4, tetrahydrobiopterin is developed by BioMarin Pharmaceutical (see full BioMarin Pharmaceutical pipeline at /company/biomarin-pharmaceutical).
What development phase is sapropterin dihydrochloride, 6R-BH4, tetrahydrobiopterin in?
sapropterin dihydrochloride, 6R-BH4, tetrahydrobiopterin is in Phase 3.