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rtPA

Hui-Sheng Chen · FDA-approved active Small molecule

rtPA is a tissue plasminogen activator that converts plasminogen to plasmin, directly dissolving fibrin clots through fibrinolysis.

rtPA is a tissue plasminogen activator that converts plasminogen to plasmin, directly dissolving fibrin clots through fibrinolysis. Used for Acute ischemic stroke (within 3–4.5 hours of symptom onset), Acute myocardial infarction, Pulmonary embolism.

At a glance

Generic namertPA
Also known asalteplase
SponsorHui-Sheng Chen
Drug classFibrinolytic agent; tissue plasminogen activator (tPA)
TargetPlasminogen; fibrin
ModalitySmall molecule
Therapeutic areaCardiovascular; Neurology
PhaseFDA-approved

Mechanism of action

rtPA binds to fibrin in thrombi and catalyzes the conversion of plasminogen to plasmin, which degrades the fibrin matrix of blood clots. This mechanism enables rapid clot dissolution in acute thrombotic conditions. rtPA is selective for fibrin-bound plasminogen, which provides some selectivity for clot lysis over systemic fibrinolysis.

Approved indications

Common side effects

Key clinical trials

Primary sources

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SourceUsed for
ClinicalTrials.govTrial enrolment, design, endpoints, results

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