PBGM01

Gemma Biotherapeutics · Phase 1 active Biologic Quality 0/100

At a glance

Generic name	PBGM01
Sponsor	Gemma Biotherapeutics
Modality	Biologic
Phase	Phase 1

Approved indications

No approved indications tracked.

Common side effects

No common side effects on file.

Key clinical trials

Study of Safety, Tolerability and Efficacy of PBGM01 in Pediatric Participants With GM1 Gangliosidosis (PHASE1, PHASE2)

Primary sources

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Source	Used for
ClinicalTrials.gov	Trial enrolment, design, endpoints, results

Competitive intelligence

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PBGM01 CI brief — competitive landscape report
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Gemma Biotherapeutics portfolio CI