EMA — authorised 24 June 2022
- Application: EMEA/H/C/004850
- Marketing authorisation holder: Sanofi B.V.
- Local brand name: Xenpozyme
- Indication: Xenpozyme is indicated as an enzyme replacement therapy for the treatment of non-Central Nervous System (CNS) manifestations of Acid Sphingomyelinase Deficiency (ASMD) in paediatric and adult patients with type A/B or type B.
- Pathway: orphan, PRIME
- Status: approved