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OCTA-C1-INH

Octapharma · Phase 3 active Small molecule

OCTA-C1-INH is a recombinant C1-esterase inhibitor that replaces or augments deficient or dysfunctional C1-inhibitor protein to prevent excessive complement and contact system activation.

OCTA-C1-INH is a recombinant C1-esterase inhibitor that replaces or augments deficient or dysfunctional C1-inhibitor protein to prevent excessive complement and contact system activation. Used for Hereditary angioedema (HAE) due to C1-inhibitor deficiency or dysfunction.

At a glance

Generic nameOCTA-C1-INH
SponsorOctapharma
Drug classRecombinant C1-esterase inhibitor
TargetC1-esterase inhibitor (C1-INH)
ModalitySmall molecule
Therapeutic areaImmunology / Rare Disease
PhasePhase 3

Mechanism of action

C1-inhibitor is a serine protease inhibitor that regulates the classical complement pathway and contact system (kallikrein-kinin pathway). Deficiency or dysfunction of C1-INH leads to uncontrolled activation of these cascades, resulting in excessive bradykinin production and angioedema. OCTA-C1-INH restores normal inhibitory control, preventing acute attacks and reducing swelling episodes.

Approved indications

Common side effects

Key clinical trials

Primary sources

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SourceUsed for
ClinicalTrials.govTrial enrolment, design, endpoints, results

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