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OBI-999

OBI Pharma, Inc · discontinued Small molecule

OBI-999 is an antibody-drug conjugate targeting Globo H carbohydrate antigen on cancer cells to deliver cytotoxic payload.

OBI-999 is a Globo H-targeting antibody-drug conjugate (ADC) developed by OBI Pharma for advanced solid tumors. The drug works by binding to Globo H, a carbohydrate antigen overexpressed on cancer cells, and delivering a cytotoxic payload to induce tumor cell death. OBI-999 entered clinical development with a first-in-human study published in JCO Precision Oncology (2023), demonstrating preliminary activity in patients with advanced solid tumors. The program has been discontinued, indicating the company did not advance the asset to later-stage development or chose to reallocate resources. As a Globo H-targeting ADC, OBI-999 represented a differentiated approach to solid tumor treatment, though clinical efficacy or safety concerns likely contributed to the discontinuation decision. The asset remains notable in the ADC landscape as an example of carbohydrate antigen targeting in oncology.

At a glance

Generic nameOBI-999
SponsorOBI Pharma, Inc
Drug classAntibody-drug conjugate (ADC)
TargetGlobo H (globoside carbohydrate antigen)
ModalitySmall molecule
Therapeutic areaOncology
Phasediscontinued

Mechanism of action

OBI-999 functions as an antibody-drug conjugate (ADC), a biotherapeutic combining monoclonal antibody specificity with chemotherapy potency. The antibody component recognizes and binds to Globo H, a carbohydrate antigen that is overexpressed on the surface of many advanced solid tumors but has limited expression on normal tissues. Once the OBI-999 antibody binds to Globo H on tumor cells, the complex is internalized through receptor-mediated endocytosis. Inside the cell, the linker connecting the antibody to the cytotoxic payload is cleaved, releasing the active drug to disrupt microtubule dynamics and induce apoptosis. This mechanism allows selective delivery of chemotherapy to tumor cells while minimizing exposure to healthy tissue, potentially improving the therapeutic window compared to conventional chemotherapy.

Approved indications

No approved indications tracked.

Pipeline indications

Common side effects

No common side effects on file.

Key clinical trials

Primary sources

Every claim on this page is sourced from regulatory or scientific primary sources. See our editorial policy for full methodology.

SourceUsed for
ClinicalTrials.govTrial enrolment, design, endpoints, results

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