Last reviewed · How we verify

NUSINERSEN SODIUM

FDA-approved approved Oligonucleotide ✓ Verified May 2026 Quality 1/100

NUSINERSEN SODIUM is a drug. It is currently FDA-approved (first approved 2016).

Nusinersen sodium is an oligonucleotide that acts as a positive modulator of SMN2 pre-mRNA. It is used to treat muscular atrophy, specifically spinal muscular atrophy, as indicated by clinical trials.

At a glance

Generic nameNUSINERSEN SODIUM
ModalityOligonucleotide
PhaseFDA-approved
First approval2016

Approved indications

No approved indications tracked.

Common side effects

No common side effects on file.

Key clinical trials

Primary sources

Every claim on this page is sourced from regulatory or scientific primary sources. See our editorial policy for full methodology.

SourceUsed for
FDA labelMechanism, indications, dosing, boxed warnings, drug interactions
ClinicalTrials.govTrial enrolment, design, endpoints, results

Competitive intelligence

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Frequently asked questions about NUSINERSEN SODIUM

What is NUSINERSEN SODIUM?

NUSINERSEN SODIUM is a Oligonucleotide drug.

When was NUSINERSEN SODIUM approved?

NUSINERSEN SODIUM was first approved on 2016.

What development phase is NUSINERSEN SODIUM in?

NUSINERSEN SODIUM is FDA-approved (marketed).

Related

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing