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Zejula (niraparib)
Zejula works by blocking the action of an enzyme called PARP, which helps repair damaged DNA in cancer cells.
At a glance
| Generic name | niraparib |
|---|---|
| Sponsor | GSK |
| Drug class | Poly(ADP-Ribose) Polymerase Inhibitor |
| Target | Poly [ADP-ribose] polymerase 2 |
| Therapeutic area | Oncology |
| Phase | FDA-approved |
| First approval | 2017 |
| Annual revenue | 600 |
Mechanism of action
Niraparib is an inhibitor of PARP enzymes, including PARP-1 and PARP-2, that play role in DNA repair. In vitro studies have shown that niraparib-induced cytotoxicity may involve inhibition of PARP enzymatic activity and increased formation of PARP-DNA complexes resulting in DNA damage, apoptosis, and cell death. Increased niraparib-induced cytotoxicity was observed in tumor cell lines with or without deficiencies in BRCA1/2. Niraparib decreased tumor growth in mouse xenograft models of human cancer cell lines with deficiencies in BRCA1/2 and in human patient-derived xenograft tumor models with HRD that had either mutated or wild-type BRCA1/2.
Approved indications
- Carcinoma in situ of fallopian tube
- Hormone refractory prostate cancer
- Malignant epithelial tumor of ovary
- Malignant tumor of ovary
- Malignant tumor of peritoneum
Common side effects
- Nausea
- Thrombocytopenia
- Anemia
- Fatigue
- Constipation
- Musculoskeletal pain
- Abdominal pain
- Vomiting
- Neutropenia
- Decreased appetite
- Leukopenia
- Insomnia
Key clinical trials
- A Study of Niraparib in Patients With Ovarian Cancer Who Have Received Three or Four Previous Chemotherapy Regimens (PHASE2)
- A Maintenance Study With Niraparib Versus Placebo in Patients With Platinum Sensitive Ovarian Cancer (PHASE3)
- A Phase I/II Study of WJB001 Combination Therapy on Safety and Efficacy for Advanced Solid Tumors (PHASE1,PHASE2)
- Combination Niraparib and Dostarlimab Therapy for Recurrent or Persistent Uterine Serous Carcinoma (PHASE2)
- Liquid-biopsy Informed Platform Trial to Evaluate CDK4/6-inhibitor Resistant ER+/HER2- Metastatic Breast Cancer (PHASE2)
- A Study of Niraparib Combination Therapies for the Treatment of Metastatic Castration-Resistant Prostate Cancer (PHASE2)
- Niraparib in Patients With Pancreatic Cancer (PHASE2)
- Phase 3 Trial Evaluating the Safety & Efficacy of IMNN-001 Administered in Combination w/ Standard NACT & Adjuvant Chemotherapy in Newly Diagnosed Patients w/ Advanced EOC, Fallopian Tube or Primary Peritoneal Cancer (PHASE3)
Patents
| Patent | Expiry | Type |
|---|---|---|
Primary sources
Every claim on this page is sourced from regulatory or scientific primary sources. See our editorial policy for full methodology.
| Source | Used for |
|---|---|
| FDA label | Mechanism, indications, dosing, boxed warnings, drug interactions |
| ClinicalTrials.gov | Trial enrolment, design, endpoints, results |
| FDA Orange Book | Patents + exclusivity |
| SEC EDGAR | Revenue + earnings |