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Myozyme ›
Regulatory · United States
Marketing authorisations
FDA — authorised 28 April 2006
Application: BLA125141
Marketing authorisation holder: GENZYME
Local brand name: MYOZYME
Indication: INJECTABLE — IV (INFUSION)
Status: approved
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FDA
Safety signals — FAERS
Adverse reaction reports describe suspected side effects. A report does not mean the drug caused the event — co-medications, underlying disease and coincidence all contribute.
Window: 20 April 2025 – 20 April 2026
Total reports: 1,524
Most-reported reactions
Respiratory Failure — 242 reports (15.88%) Pyrexia — 218 reports (14.3%) Pneumonia — 199 reports (13.06%) Death — 177 reports (11.61%) Disease Progression — 154 reports (10.1%) Dyspnoea — 136 reports (8.92%) Oxygen Saturation Decreased — 105 reports (6.89%) Respiratory Distress — 104 reports (6.82%) Cardiac Failure — 101 reports (6.63%) Infusion Related Reaction — 88 reports (5.77%)
Source database →
Myozyme in other countries
Same drug, different regulators. Each page below lists the local marketing authorisation, HTA position, pricing, and adverse-event data.
Other Rare Disease approved in United States
Frequently asked questions
Is Myozyme approved in United States?
Yes. FDA authorised it on 28 April 2006; FDA has authorised it.
Who is the marketing authorisation holder for Myozyme in United States?
GENZYME holds the US marketing authorisation.